Fanconi Anemia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2024-07-25Clinical Trial Update: Safety and Efficacy of Metformin for Treatment of Cytopenia in Children and Adolescents With Fanconi Anemia [Phase 3]
A Phase 3 clinical trial update assessing the safety and efficacy of metformin for treating cytopenia in children and adolescents with Fanco…
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CLINICAL_TRIALS trial_result · 2024-07-24Clinical Trial Update: Time-restricted Feeding to Reduce Inflammation in Fanconi Anemia [NA]
A completed clinical trial assessing whether time-restricted feeding can reduce inflammation in individuals with Fanconi anemia.
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CLINICAL_TRIALS trial_result · 2024-07-08Clinical Trial Update: Prognostic Significance of Mutation Type and Chromosome Fragility in Fanconi Anemia
This clinical trial update examines the prognostic significance of mutation type and chromosome fragility in Fanconi anemia. The study is co…
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CLINICAL_TRIALS trial_result · 2024-05-22Clinical Trial Update: Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype A [Phase 2]
This is an update on a Phase 2 lentiviral gene therapy trial for pediatric patients with Fanconi anemia group A, currently active but not re…
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CLINICAL_TRIALS trial_result · 2024-05-17Clinical Trial Update: Gene Therapy for Fanconi Anemia [Phase 1]
A Phase 1 gene therapy trial for Fanconi Anemia was terminated; no efficacy results are reported in the update.
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CLINICAL_TRIALS trial_result · 2024-03-21Clinical Trial Update: Lentiviral-mediated Gene Therapy of Fanconi Anemia Patients Subtype A [Phase 1, Phase 2]
Phase 1/2 trial of lentiviral-mediated gene therapy for Fanconi Anemia Type A has completed.
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CLINICAL_TRIALS trial_result · 2023-09-26Clinical Trial Update: Long Term Follow-up Study for Patients Enrolled on the BP-004 Clinical Study [Phase 1, Phase 2]
Long-term follow-up update from BP-004 study (Phase 1/Phase 2) by Bellicum Pharmaceuticals; study status TERMINATED with results posted in 2…
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CLINICAL_TRIALS trial_result · 2023-09-21Clinical Trial Update: Eltrombopag for Treatment of Fanconi Anemia [Phase 2]
A Phase 2 clinical trial evaluated eltrombopag for Fanconi Anemia and has completed.
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CLINICAL_TRIALS trial_result · 2023-01-04Clinical Trial Update: Safety Study of Gene Modified Donor T-cells Following TCRαβ+ Depleted Stem Cell Transplant [Phase 1, Phase 2]
A phase 1/2 safety study evaluating gene-modified donor T-cells after TCRαβ+ depleted stem cell transplant was terminated; results were post…
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CLINICAL_TRIALS trial_result · 2022-11-29Clinical Trial Update: Pilot Study of Metformin for Patients With Fanconi Anemia [Phase 2]
Pilot Phase 2 trial assessing metformin in patients with Fanconi Anemia has completed with results posted.
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CLINICAL_TRIALS trial_result · 2022-04-12Clinical Trial Update: A Study of the Effect of Blood Stem Cell Transplant After Chemotherapy Alone in Patients With Fanconi Anemia [Phase 2]
Phase 2 trial assessing the effect of blood stem cell transplant after chemotherapy in Fanconi Anemia; study terminated with posted results.
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CLINICAL_TRIALS trial_result · 2021-12-02Clinical Trial Update: Hematopoietic Stem Cell Transplantation in High Risk Patients With Fanconi Anemia [Phase 2]
Phase 2 clinical trial update on hematopoietic stem cell transplantation in high-risk Fanconi anemia patients; study completed with results …
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CLINICAL_TRIALS trial_result · 2021-11-24Clinical Trial Update: TBI Dose De-escalation for Fanconi Anemia [Phase 2, Phase 3]
Clinical trial update on dose de-escalation of total body irradiation (TBI) for Fanconi Anemia, completed with results posted in 2021.
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CLINICAL_TRIALS trial_result · 2021-10-12Clinical Trial Update: Cytoxan, Fludara, and Antithymocyte Globulin Conditioning Followed By Stem Cell Transplant in Treating Fanconi Anemia [Phase 1, Phase 2]
Phase 1/2 trial evaluating Cytoxan, Fludara, and Antithymocyte Globulin conditioning followed by stem cell transplant in Fanconi Anemia has …
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CLINICAL_TRIALS trial_result · 2020-10-30Clinical Trial Update: Mobilization and Collection of Peripheral Blood Stem Cells in Patients With Fanconi Anemia Using G-CSF and AMD3100 [Phase 1, Phase 2]
Phase 1/2 trial evaluating mobilization and collection of peripheral blood stem cells in Fanconi anemia patients using G-CSF and AMD3100; tr…
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CLINICAL_TRIALS trial_result · 2020-05-27Clinical Trial Update: Clinical Phase II Trial to Evaluate CD34+ Cells Mobilization and Collection in Patients With Fanconi Anemia for Subsequent Transduction With a Lentiviral Vector Carring FANCA Gene. FANCOSTEM-1 [Phase 2]
Phase II clinical trial evaluating CD34+ cell mobilization and collection in Fanconi anemia patients for subsequent FANCA gene transduction …
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CLINICAL_TRIALS trial_result · 2020-02-10Clinical Trial Update: NMA Allogeneic Hematopoietic Cell Transplant in Hematologic Cancer/Disorders [Phase 2]
Phase 2 trial update of an allogeneic hematopoietic cell transplant in hematologic cancers/disorders; status completed with results posted i…
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CLINICAL_TRIALS trial_result · 2019-09-11Clinical Trial Update: Hematopoietic Stem Cell Transplant for Fanconi Anemia [Phase 2]
Phase 2 trial update on hematopoietic stem cell transplant for Fanconi Anemia completed.
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CLINICAL_TRIALS trial_result · 2019-02-19Clinical Trial Update: Safety and Efficacy Trial of Danazol in Patients With Fanconi Anemia or Dyskeratosis Congenita [Phase 1, Phase 2]
The Phase 1/2 safety and efficacy trial of danazol in patients with Fanconi anemia or Dyskeratosis Congenita was terminated, and results hav…
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CLINICAL_TRIALS trial_result · 2018-07-10Clinical Trial Update: Hematopoietic Stem Cell Transplantation for the Treatment of Patients With Fanconi Anemia Lacking a Genotypically Identical Donor, Using a Chemotherapy Only Cytoreduction With Busulfan, Cyclophosphamide and Fludarabine [Phase 2]
Phase 2 trial evaluating hematopoietic stem cell transplantation after a chemotherapy-only cytoreduction with busulfan, cyclophosphamide, an…
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CLINICAL_TRIALS trial_result · 2017-12-04Clinical Trial Update: Gene Function in Bone Marrow Cells From Patients With Fanconi Anemia and From Healthy Participants
A terminated clinical trial update examining gene function in bone marrow cells from patients with Fanconi anemia and from healthy participa…
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CLINICAL_TRIALS research · 2017-12-04Clinical Trial Update: Tissue Sample Collection From Patients With Fanconi Anemia
This clinical trial update documents tissue sample collection from patients with Fanconi anemia; the study is completed.
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CLINICAL_TRIALS trial_result · 2017-12-04Clinical Trial Update: Evaluating Cell Damage in Patients With Acute Myeloid Leukemia, Myelodysplastic Syndromes, or Fanconi Anemia; in Patients Who Were Exposed to Alkylating Agents; and in Healthy Volunteers
A completed clinical trial evaluating cell damage from alkylating agents in patients with acute myeloid leukemia, myelodysplastic syndromes,…
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CLINICAL_TRIALS trial_result · 2017-11-29Clinical Trial Update: Donor Umbilical Cord Blood Transplant in Treating Patients With Hematologic Cancer [NA]
ClinicalTrials.gov entry describes termination of a study evaluating donor umbilical cord blood transplantation for various hematologic canc…
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CLINICAL_TRIALS trial_result · 2017-08-22Clinical Trial Update: Study of Deferasirox in Iron Overload From Beta-thalassemia Unable to be Treated With Deferoxamine or Chronic Anemias [Phase 2]
Phase 2 study of deferasirox for iron overload in beta-thalassemia patients who cannot be treated with deferoxamine, as well as related chro…