Fanconi Anemia
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EMA withdrawal · 2025-10-27EMA Application withdrawn: Fanskya (mozafancogene autotemcel) — Rocket Pharmaceuticals B.V.
The European Medicines Agency has withdrawn the marketing authorization application for Fanskya (mozafancogene autotemcel) intended to treat…
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CLINICAL_TRIALS withdrawal · 2025-03-06Clinical Trial Update: A Dose Escalation Study of FP-045 in Patients With Fanconi Anemia [Phase 1, Phase 2]
A dose-escalation study of FP-045 in patients with Fanconi Anemia has been withdrawn (Phase 1/Phase 2).
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CLINICAL_TRIALS withdrawal · 2017-07-11Clinical Trial Update: Unrelated HSCT in Patients With Fanconi Anemia [NA]
A clinical trial investigating unrelated hematopoietic stem cell transplantation in patients with Fanconi anemia has been withdrawn.