Fanconi Anemia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Experience and Management of Cancer Screening-Related Anxiety in Fanconi Anemia
An ongoing study sponsored by the National Cancer Institute examines how individuals with Fanconi anemia experience and manage anxiety relat…
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Clinical Genetics Branch Eligibility Screening Survey
National Cancer Institute conducts an eligibility screening survey for a clinical trial spanning multiple cancer predisposition conditions, …
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CLINICAL_TRIALS trial_result · 2026-04-20Clinical Trial Update: Quercetin Chemoprevention for Squamous Cell Carcinoma in Patients With Fanconi Anemia [Phase 2]
Phase 2 trial evaluating quercetin for chemoprevention of squamous cell carcinoma in patients with Fanconi anemia has completed with results…
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CLINICAL_TRIALS trial_result · 2026-04-14Clinical Trial Update: Cancer in Inherited Bone Marrow Failure Syndromes
This clinical trial is currently recruiting to study cancer in inherited bone marrow failure syndromes, including Diamond Blackfan Anemia, D…
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CLINICAL_TRIALS research · 2026-04-14Clinical Trial Update: Long-Term Follow-up: Phase I/II Clinical Study to Evaluate the Safety and Efficacy of the Infusion of RP-L102
This clinical trial update describes the long-term follow-up of the Phase I/II infusion of RP-L102 in Fanconi Anemia. Enrollment is by invit…
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CLINICAL_TRIALS trial_result · 2026-04-13Clinical Trial Update: Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy
This clinical trial update reports long-term follow-up of subjects with Fanconi anemia type A treated with ex vivo gene therapy, with the st…
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CLINICAL_TRIALS research · 2026-03-17Clinical Trial Update: Defining the Natural History of Squamous Cell Carcinoma in Fanconi Anemia
Clinical trial aiming to define the natural history of squamous cell carcinoma in people with Fanconi anemia and inherited bone marrow failu…
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CLINICAL_TRIALS trial_result · 2026-03-05Clinical Trial Update: Widefield Fluorescence and Reflectance Imaging Systems and Oral Tissue Samples in Monitoring Participants at Risk for Developing Oral Cancer [NA]
A clinical trial (NCT00542373) is evaluating widefield fluorescence and reflectance imaging systems and oral tissue samples to monitor indiv…
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CLINICAL_TRIALS research · 2026-02-19Clinical Trial Update: Prenatal Transplantation for Fetuses With Fanconi Anemia [Phase 1, Phase 2]
This is a Phase 1/2 clinical trial update on prenatal transplantation for fetuses with Fanconi anemia. The study status is NOT_YET_RECRUITIN…
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CLINICAL_TRIALS research · 2026-02-18Clinical Trial Update: Expanded Access to CD34+ Selection Utilizing Miltenyi CliniMACS Prodigy® for Patients Receiving Peripheral Blood Stem Cell Transplantations and Stem Cell Boosts
This clinical trial update describes expanded access to CD34+ selection using the Miltenyi CliniMACS Prodigy for patients receiving peripher…
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CLINICAL_TRIALS research · 2026-01-30Clinical Trial Update: Alpha/Beta TCD HCT in Patients With Inherited BMF Disorders [Phase 2]
Phase 2 clinical trial update investigating alpha/beta T cell receptor alpha/beta-depleted hematopoietic cell transplantation in inherited b…
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CLINICAL_TRIALS research · 2026-01-27Clinical Trial Update: Depleted Donor Stem Cell Transplant in Children and Adults With Fanconi Anemia After Being Conditioned With a Regimen Containing Briquilimab [Phase 1, Phase 2]
A Phase 1/2 clinical trial is evaluating depleted donor stem cell transplantation in children and adults with Fanconi anemia using a conditi…
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CLINICAL_TRIALS research · 2025-12-22Clinical Trial Update: Gene Therapy for Fanconi Anemia, Complementation Group A [Phase 2]
This entry reports a Phase 2 gene therapy trial for Fanconi anemia, complementation group A, which is currently active but not recruiting.
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CLINICAL_TRIALS research · 2025-11-28Clinical Trial Update: Regenerative Medicine to Restore Hematopoiesis and Immune Function in Immunodeficiencies and Inherited Bone Marrow Failures [Phase 2]
Phase 2 clinical trial update on regenerative medicine to restore hematopoiesis and immune function in immunodeficiencies and inherited bone…
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CLINICAL_TRIALS research · 2025-11-21Clinical Trial Update: Non-invasive Characterisation of Oral Carcinomas in Patients With Fanconi Anaemia [NA]
This clinical trial update describes a study to non-invasively characterize oral carcinomas in patients with Fanconi anemia, with recruitmen…
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CLINICAL_TRIALS research · 2025-11-12Clinical Trial Update: HSCT for Patients With Fanconi Anemia Using Risk-Adjusted Chemotherapy [Phase 2]
Phase 2 trial evaluating hematopoietic stem cell transplantation using risk-adjusted chemotherapy for patients with Fanconi anemia and sever…
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CLINICAL_TRIALS research · 2025-11-04Clinical Trial Update: Investigation of the Genetics of Hematologic Diseases
A St. Jude-sponsored clinical trial update indicates a study on the genetics of hematologic diseases is currently recruiting, covering sever…
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EMA withdrawal · 2025-10-27EMA Application withdrawn: Fanskya (mozafancogene autotemcel) — Rocket Pharmaceuticals B.V.
The European Medicines Agency has withdrawn the marketing authorization application for Fanskya (mozafancogene autotemcel) intended to treat…
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CLINICAL_TRIALS trial_result · 2025-09-11Clinical Trial Update: Mobilization and Collection of Peripheral Blood Stem Cells in Patients With Fanconi Anemia Using G-CSF and Plerixafor [Phase 1, Phase 2]
A Phase 1/2 trial evaluating mobilization and collection of peripheral blood stem cells in Fanconi anemia patients using G-CSF with plerixaf…
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CLINICAL_TRIALS trial_result · 2025-08-24Clinical Trial Update: Eltrombopag for People With Fanconi Anemia [Phase 2]
A phase 2 clinical trial of eltrombopag for people with Fanconi anemia is currently active but not recruiting.
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CLINICAL_TRIALS research · 2025-08-22Clinical Trial Update: Role of Acetaldehyde in the Development of Oral Cancer [NA]
A clinical trial sponsored by the Masonic Cancer Center is exploring the role of acetaldehyde in the development of oral cancer; the study i…
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CLINICAL_TRIALS research · 2025-08-12Clinical Trial Update: Corrective Exercise and Rehabilitation in Fanconi Anemia: A Case Study [NA]
This clinical trial update presents a case study on corrective exercise and rehabilitation for Fanconi Anemia, outlining the approach and ob…
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CLINICAL_TRIALS withdrawal · 2025-03-06Clinical Trial Update: A Dose Escalation Study of FP-045 in Patients With Fanconi Anemia [Phase 1, Phase 2]
A dose-escalation study of FP-045 in patients with Fanconi Anemia has been withdrawn (Phase 1/Phase 2).
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CLINICAL_TRIALS research · 2024-11-20Clinical Trial Update: Afatinib in Patients with Fanconi Anemia (FA) and Advanced Head and Neck Squamous Cell Carcinoma (HNSCC) [Phase 1, Phase 2]
A phase 1/2 clinical trial evaluating afatinib for patients with Fanconi anemia and advanced head and neck squamous cell carcinoma is curren…
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CLINICAL_TRIALS trial_result · 2024-10-31Clinical Trial Update: Risk-Adapted Allogeneic Stem Cell Transplantation For Mixed Donor Chimerism In Patients With Non-Malignant Diseases [Phase 2, Phase 3]
Clinical trial update reports Phase 2 and Phase 3 results for risk-adapted allogeneic stem cell transplantation in non-malignant diseases wi…