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CLINICAL_TRIALS trial_result · 2024-03-21

Clinical Trial Update: Lentiviral-mediated Gene Therapy of Fanconi Anemia Patients Subtype A [Phase 1, Phase 2]

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Summary

Phase 1/2 trial of lentiviral-mediated gene therapy for Fanconi Anemia Type A has completed.

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Diseases / indications

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Sponsor: Hospital Infantil Universitario Niño Jesús, Madrid, Spain | Conditions: Fanconi Anemia | Phase 1, Phase 2 | Status: COMPLETED