Clinical Trial Update: Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype A [Phase 2]

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Summary

This is an update on a Phase 2 lentiviral gene therapy trial for pediatric patients with Fanconi anemia group A, currently active but not recruiting.

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Diseases / indications

• Fanconi Anemia
• Fanconi Anemia Complementation Group

Drugs mentioned

• Lentiviral-mediated gene therapy for Fanconi anemia A (Lentiviral gene therapy)

Snippet

Sponsor: Rocket Pharmaceuticals Inc. | Conditions: Fanconi Anemia Complementation Group A | Phase 2 | Status: ACTIVE_NOT_RECRUITING