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CLINICAL_TRIALS trial_result · 2020-05-27

Clinical Trial Update: Clinical Phase II Trial to Evaluate CD34+ Cells Mobilization and Collection in Patients With Fanconi Anemia for Subsequent Transduction With a Lentiviral Vector Carring FANCA Gene. FANCOSTEM-1 [Phase 2]

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Summary

Phase II clinical trial evaluating CD34+ cell mobilization and collection in Fanconi anemia patients for subsequent FANCA gene transduction using a lentiviral v…

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Sponsor: Hospital Universitari Vall d'Hebron Research Institute | Conditions: Fanconi Anemia | Phase 2 | Status: COMPLETED