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CLINICAL_TRIALS trial_result · 2024-05-17

Clinical Trial Update: Gene Therapy for Fanconi Anemia [Phase 1]

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Summary

A Phase 1 gene therapy trial for Fanconi Anemia was terminated; no efficacy results are reported in the update.

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Diseases / indications

Drugs mentioned

  • Fanconi Anemia Gene Therapy (investigational)

Snippet

Sponsor: Fred Hutchinson Cancer Center | Conditions: Fanconi Anemia | Phase 1 | Status: TERMINATED