Fanconi Anemia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2026-04-20Clinical Trial Update: Quercetin Chemoprevention for Squamous Cell Carcinoma in Patients With Fanconi Anemia [Phase 2]
Phase 2 trial evaluating quercetin for chemoprevention of squamous cell carcinoma in patients with Fanconi anemia has completed with results…
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CLINICAL_TRIALS trial_result · 2026-04-14Clinical Trial Update: Cancer in Inherited Bone Marrow Failure Syndromes
This clinical trial is currently recruiting to study cancer in inherited bone marrow failure syndromes, including Diamond Blackfan Anemia, D…
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CLINICAL_TRIALS trial_result · 2026-04-13Clinical Trial Update: Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy
This clinical trial update reports long-term follow-up of subjects with Fanconi anemia type A treated with ex vivo gene therapy, with the st…
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CLINICAL_TRIALS trial_result · 2026-03-05Clinical Trial Update: Widefield Fluorescence and Reflectance Imaging Systems and Oral Tissue Samples in Monitoring Participants at Risk for Developing Oral Cancer [NA]
A clinical trial (NCT00542373) is evaluating widefield fluorescence and reflectance imaging systems and oral tissue samples to monitor indiv…
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CLINICAL_TRIALS trial_result · 2025-09-11Clinical Trial Update: Mobilization and Collection of Peripheral Blood Stem Cells in Patients With Fanconi Anemia Using G-CSF and Plerixafor [Phase 1, Phase 2]
A Phase 1/2 trial evaluating mobilization and collection of peripheral blood stem cells in Fanconi anemia patients using G-CSF with plerixaf…
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CLINICAL_TRIALS trial_result · 2025-08-24Clinical Trial Update: Eltrombopag for People With Fanconi Anemia [Phase 2]
A phase 2 clinical trial of eltrombopag for people with Fanconi anemia is currently active but not recruiting.
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CLINICAL_TRIALS trial_result · 2024-10-31Clinical Trial Update: Risk-Adapted Allogeneic Stem Cell Transplantation For Mixed Donor Chimerism In Patients With Non-Malignant Diseases [Phase 2, Phase 3]
Clinical trial update reports Phase 2 and Phase 3 results for risk-adapted allogeneic stem cell transplantation in non-malignant diseases wi…
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CLINICAL_TRIALS trial_result · 2024-07-25Clinical Trial Update: Safety and Efficacy of Metformin for Treatment of Cytopenia in Children and Adolescents With Fanconi Anemia [Phase 3]
A Phase 3 clinical trial update assessing the safety and efficacy of metformin for treating cytopenia in children and adolescents with Fanco…
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CLINICAL_TRIALS trial_result · 2024-07-24Clinical Trial Update: Time-restricted Feeding to Reduce Inflammation in Fanconi Anemia [NA]
A completed clinical trial assessing whether time-restricted feeding can reduce inflammation in individuals with Fanconi anemia.
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CLINICAL_TRIALS trial_result · 2024-07-08Clinical Trial Update: Prognostic Significance of Mutation Type and Chromosome Fragility in Fanconi Anemia
This clinical trial update examines the prognostic significance of mutation type and chromosome fragility in Fanconi anemia. The study is co…
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CLINICAL_TRIALS trial_result · 2024-05-22Clinical Trial Update: Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype A [Phase 2]
This is an update on a Phase 2 lentiviral gene therapy trial for pediatric patients with Fanconi anemia group A, currently active but not re…
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CLINICAL_TRIALS trial_result · 2024-05-17Clinical Trial Update: Gene Therapy for Fanconi Anemia [Phase 1]
A Phase 1 gene therapy trial for Fanconi Anemia was terminated; no efficacy results are reported in the update.
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CLINICAL_TRIALS trial_result · 2024-03-21Clinical Trial Update: Lentiviral-mediated Gene Therapy of Fanconi Anemia Patients Subtype A [Phase 1, Phase 2]
Phase 1/2 trial of lentiviral-mediated gene therapy for Fanconi Anemia Type A has completed.
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CLINICAL_TRIALS trial_result · 2023-09-26Clinical Trial Update: Long Term Follow-up Study for Patients Enrolled on the BP-004 Clinical Study [Phase 1, Phase 2]
Long-term follow-up update from BP-004 study (Phase 1/Phase 2) by Bellicum Pharmaceuticals; study status TERMINATED with results posted in 2…
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CLINICAL_TRIALS trial_result · 2023-09-21Clinical Trial Update: Eltrombopag for Treatment of Fanconi Anemia [Phase 2]
A Phase 2 clinical trial evaluated eltrombopag for Fanconi Anemia and has completed.
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CLINICAL_TRIALS trial_result · 2023-01-04Clinical Trial Update: Safety Study of Gene Modified Donor T-cells Following TCRαβ+ Depleted Stem Cell Transplant [Phase 1, Phase 2]
A phase 1/2 safety study evaluating gene-modified donor T-cells after TCRαβ+ depleted stem cell transplant was terminated; results were post…
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CLINICAL_TRIALS trial_result · 2022-11-29Clinical Trial Update: Pilot Study of Metformin for Patients With Fanconi Anemia [Phase 2]
Pilot Phase 2 trial assessing metformin in patients with Fanconi Anemia has completed with results posted.
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CLINICAL_TRIALS trial_result · 2022-04-12Clinical Trial Update: A Study of the Effect of Blood Stem Cell Transplant After Chemotherapy Alone in Patients With Fanconi Anemia [Phase 2]
Phase 2 trial assessing the effect of blood stem cell transplant after chemotherapy in Fanconi Anemia; study terminated with posted results.
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CLINICAL_TRIALS trial_result · 2021-12-02Clinical Trial Update: Hematopoietic Stem Cell Transplantation in High Risk Patients With Fanconi Anemia [Phase 2]
Phase 2 clinical trial update on hematopoietic stem cell transplantation in high-risk Fanconi anemia patients; study completed with results …
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CLINICAL_TRIALS trial_result · 2021-11-24Clinical Trial Update: TBI Dose De-escalation for Fanconi Anemia [Phase 2, Phase 3]
Clinical trial update on dose de-escalation of total body irradiation (TBI) for Fanconi Anemia, completed with results posted in 2021.
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CLINICAL_TRIALS trial_result · 2021-10-12Clinical Trial Update: Cytoxan, Fludara, and Antithymocyte Globulin Conditioning Followed By Stem Cell Transplant in Treating Fanconi Anemia [Phase 1, Phase 2]
Phase 1/2 trial evaluating Cytoxan, Fludara, and Antithymocyte Globulin conditioning followed by stem cell transplant in Fanconi Anemia has …
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CLINICAL_TRIALS trial_result · 2020-10-30Clinical Trial Update: Mobilization and Collection of Peripheral Blood Stem Cells in Patients With Fanconi Anemia Using G-CSF and AMD3100 [Phase 1, Phase 2]
Phase 1/2 trial evaluating mobilization and collection of peripheral blood stem cells in Fanconi anemia patients using G-CSF and AMD3100; tr…
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CLINICAL_TRIALS trial_result · 2020-05-27Clinical Trial Update: Clinical Phase II Trial to Evaluate CD34+ Cells Mobilization and Collection in Patients With Fanconi Anemia for Subsequent Transduction With a Lentiviral Vector Carring FANCA Gene. FANCOSTEM-1 [Phase 2]
Phase II clinical trial evaluating CD34+ cell mobilization and collection in Fanconi anemia patients for subsequent FANCA gene transduction …
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CLINICAL_TRIALS trial_result · 2020-02-10Clinical Trial Update: NMA Allogeneic Hematopoietic Cell Transplant in Hematologic Cancer/Disorders [Phase 2]
Phase 2 trial update of an allogeneic hematopoietic cell transplant in hematologic cancers/disorders; status completed with results posted i…
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CLINICAL_TRIALS trial_result · 2019-09-11Clinical Trial Update: Hematopoietic Stem Cell Transplant for Fanconi Anemia [Phase 2]
Phase 2 trial update on hematopoietic stem cell transplant for Fanconi Anemia completed.