Clinical Trial Update: Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy

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Summary

This clinical trial update reports long-term follow-up of subjects with Fanconi anemia type A treated with ex vivo gene therapy, with the study status listed as…

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Diseases / indications

• Fanconi Anemia

Drugs mentioned

• RP-L102

Snippet

Sponsor: Rocket Pharmaceuticals Inc. | Conditions: Fanconi Anemia Complementation Group A, Fanconi Anemia | Status: ACTIVE_NOT_RECRUITING