X-linked Severe Combined Immunodeficiency

• CLINICAL_TRIALS research · 2026-04-24
  Clinical Trial Update: Lentiviral Gene Transfer for Treatment of Children Older Than Two Years of Age With X-Linked Severe Combined Immunodeficiency (XSCID) [Phase 1, Phase 2]

  A Phase 1/2 clinical trial investigating lentiviral gene transfer for treating X-linked severe combined immunodeficiency in children over tw…

• CLINICAL_TRIALS research · 2026-04-02
  Clinical Trial Update: Evaluation of Patients With Immune Function Abnormalities

  The NIAID-sponsored study evaluating patients with immune function abnormalities (chronic granulomatous disease, X-linked severe combined im…

• CLINICAL_TRIALS research · 2026-02-17
  Clinical Trial Update: Base-Edited Hematopoietic Stem/Progenitor Cell X-Linked Severe Combined Immunodeficiency Gene Therapy [Phase 1, Phase 2]

  A Phase 1/2 clinical trial is evaluating a base-edited hematopoietic stem/progenitor cell gene therapy for X-linked severe combined immunode…

• CLINICAL_TRIALS research · 2025-12-11
  Clinical Trial Update: Phase I/II Trial of Lentiviral Gene Transfer for SCID-X1 With Low Dose Targeted Busulfan Conditioning [Phase 1, Phase 2]

  Phase I/II trial evaluating lentiviral gene transfer for X-linked severe combined immunodeficiency (SCID-X1) with low-dose busulfan conditio…

• CLINICAL_TRIALS research · 2025-11-10
  Clinical Trial Update: Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants [Phase 1, Phase 2]

  A gene transfer trial for X-linked severe combined immunodeficiency in newly diagnosed infants has been suspended.

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• CLINICAL_TRIALS research · 2017-08-01
  Clinical Trial Update: Gene Therapy for X-linked Severe Combined Immunodeficiency (SCID-X1) [NA]

  A clinical trial update on a gene therapy for X-linked Severe Combined Immunodeficiency (SCID-X1). The current status and phase information …