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CLINICAL_TRIALS research · 2025-11-10

Clinical Trial Update: Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants [Phase 1, Phase 2]

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Summary

A gene transfer trial for X-linked severe combined immunodeficiency in newly diagnosed infants has been suspended.

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Diseases / indications

Snippet

Sponsor: St. Jude Children's Research Hospital | Conditions: Severe Combined Immunodeficiency Disease, X-linked | Phase 1, Phase 2 | Status: SUSPENDED