X-linked Severe Combined Immunodeficiency
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Lentiviral Gene Transfer for Treatment of Children Older Than Two Years of Age With X-Linked Severe Combined Immunodeficiency (XSCID) [Phase 1, Phase 2]
A Phase 1/2 clinical trial investigating lentiviral gene transfer for treating X-linked severe combined immunodeficiency in children over tw…
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CLINICAL_TRIALS research · 2026-04-02Clinical Trial Update: Evaluation of Patients With Immune Function Abnormalities
The NIAID-sponsored study evaluating patients with immune function abnormalities (chronic granulomatous disease, X-linked severe combined im…
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CLINICAL_TRIALS trial_result · 2026-03-11Clinical Trial Update: Gene Therapy for X-linked Severe Combined Immunodeficiency [Phase 1, Phase 2]
This clinical trial update reports the completion of Phase 1/2 testing for a gene therapy treatment for X-linked severe combined immunodefic…
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CLINICAL_TRIALS research · 2026-02-17Clinical Trial Update: Base-Edited Hematopoietic Stem/Progenitor Cell X-Linked Severe Combined Immunodeficiency Gene Therapy [Phase 1, Phase 2]
A Phase 1/2 clinical trial is evaluating a base-edited hematopoietic stem/progenitor cell gene therapy for X-linked severe combined immunode…
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CLINICAL_TRIALS research · 2025-12-11Clinical Trial Update: Phase I/II Trial of Lentiviral Gene Transfer for SCID-X1 With Low Dose Targeted Busulfan Conditioning [Phase 1, Phase 2]
Phase I/II trial evaluating lentiviral gene transfer for X-linked severe combined immunodeficiency (SCID-X1) with low-dose busulfan conditio…
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CLINICAL_TRIALS research · 2025-11-10Clinical Trial Update: Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants [Phase 1, Phase 2]
A gene transfer trial for X-linked severe combined immunodeficiency in newly diagnosed infants has been suspended.
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CLINICAL_TRIALS trial_result · 2025-09-09Clinical Trial Update: SCID-X1 Gene Therapy Via Intravenous Lentiviral (Ivlv-X1) Injection [Phase 1, Phase 2]
A Phase 1/2 clinical trial is evaluating an intravenous lentiviral gene therapy (Ivlv-X1) for X-linked severe combined immunodeficiency (SCI…
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CLINICAL_TRIALS trial_result · 2019-12-04Clinical Trial Update: Lentiviral Gene Transfer for Treatment of Children Older Than 2 Years of Age With X-Linked Severe Combined Immunodeficiency [Phase 1, Phase 2]
A phase 1/2 clinical trial update for lentiviral gene transfer as a treatment for X-linked severe combined immunodeficiency in children over…
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CLINICAL_TRIALS research · 2017-08-01Clinical Trial Update: Gene Therapy for X-linked Severe Combined Immunodeficiency (SCID-X1) [NA]
A clinical trial update on a gene therapy for X-linked Severe Combined Immunodeficiency (SCID-X1). The current status and phase information …
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CLINICAL_TRIALS trial_result · 2017-07-02Clinical Trial Update: Stem Cell Gene Therapy to Treat X-Linked Severe Combined Immunodeficiency (XSCID) [Phase 1]
Phase 1 clinical trial update for a stem cell gene therapy targeting X-linked severe combined immunodeficiency. The study status indicates t…
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CLINICAL_TRIALS trial_result · 2017-07-02Clinical Trial Update: Influences on Female Adolescents' Decisions Regarding Testing for Carrier Status of XSCID
Clinical trial update on a NHGRI-funded study evaluating how female adolescents decide whether to pursue carrier testing for X-linked severe…
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CLINICAL_TRIALS trial_result · 2015-07-03Clinical Trial Update: Treatment for Growth Failure in Patients With X-Linked Severe Combined Immunodeficiency: Phase 2 Study of Insulin-Like Growth Factor-1 [Phase 1, Phase 2]
Phase 1/2 study evaluating insulin-like growth factor-1 for growth failure in X-linked severe combined immunodeficiency (X-SCID) was termina…