Clinical Trial Update: Phase I/II Trial of Lentiviral Gene Transfer for SCID-X1 With Low Dose Targeted Busulfan Conditioning [Phase 1, Phase 2]

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Summary

Phase I/II trial evaluating lentiviral gene transfer for X-linked severe combined immunodeficiency (SCID-X1) with low-dose busulfan conditioning is underway. Th…

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Diseases / indications

• X-linked Severe Combined Immunodeficiency

Snippet

Sponsor: David Williams | Conditions: Severe Combined Immunodeficiency, X Linked, Gene Therapy | Phase 1, Phase 2 | Status: RECRUITING