CLINICAL_TRIALS
research
· 2017-08-01
Clinical Trial Update: Gene Therapy for X-linked Severe Combined Immunodeficiency (SCID-X1) [NA]
Summary
A clinical trial update on a gene therapy for X-linked Severe Combined Immunodeficiency (SCID-X1). The current status and phase information are unknown.
Upgrade for the full analysis, importance score, and drug timeline.
Diseases / indications
Drugs mentioned
Snippet
Sponsor: Great Ormond Street Hospital for Children NHS Foundation Trust | Conditions: X-linked Severe Combined Immunodeficiency | NA | Status: UNKNOWN