Records containing: Pelizaeus-Merzbacher Disease

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CLINICAL_TRIALS study record update · 2026-04-17
Integrated Prospective and Retrospective Observational Study to Characterize Biomarkers and Disease Progression in Patients With Pelizaeus-Merzbacher Disease
CLINICAL_TRIALS study record update · 2026-02-09
Longitudinal Study of Neurodegenerative Disorders
CLINICAL_TRIALS study record update · 2025-12-12
A Phase 1b Study to Evaluate the Safety, Pharmacokinetics and Pharmacodynamics of Intrathecally Administered ION356 in Patients With Pelizaeus Merzbacher Disease
CLINICAL_TRIALS study record update · 2025-10-23
The Myelin Disorders Biorepository Project and Global Leukodystrophy Initiative Clinical Trials Network
CLINICAL_TRIALS study record update · 2025-09-08
Augmentation of Umbilical Cord Blood Transplantation for Inherited Metabolic Diseases With Intrathecal Administration of Human Umbilical Cord Blood-Derived Oligodendrocyte-Like Cells
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CLINICAL_TRIALS study record update · 2025-06-15
LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies
CLINICAL_TRIALS study record update · 2016-05-13
Long-Term Follow-Up Safety and Preliminary Efficacy Study of Human Central Nervous System Stem Cell (HuCNS-SC®) Transplantation in Subjects With Connatal Pelizaeus-Merzbacher Disease (PMD)
CLINICAL_TRIALS study record update · 2015-01-15
Phase I Study of the Safety and Preliminary Efficacy of Intracerebral Transplantation of HuCNS-SC® Cells for Connatal Pelizaeus-Merzbacher Disease (PMD)