CLINICAL_TRIALS
research
· 2026-04-17
Clinical Trial Update: Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease
Summary
Ionis Pharmaceuticals is conducting a study to characterize biomarkers and disease progression in Pelizaeus-Merzbacher Disease. The trial status is recruiting.
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Diseases / indications
Snippet
Sponsor: Ionis Pharmaceuticals, Inc. | Conditions: Pelizaeus-Merzbacher Disease | Status: RECRUITING