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CLINICAL_TRIALS research · 2026-04-17

Clinical Trial Update: Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease

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Summary

Ionis Pharmaceuticals is conducting a study to characterize biomarkers and disease progression in Pelizaeus-Merzbacher Disease. The trial status is recruiting.

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Diseases / indications

Snippet

Sponsor: Ionis Pharmaceuticals, Inc. | Conditions: Pelizaeus-Merzbacher Disease | Status: RECRUITING