Clinical Trial Update: Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD) [Phase 1]

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Summary

A Phase 1 clinical trial evaluating the safety, pharmacokinetics, and pharmacodynamics of intrathecally administered ION356 in participants with Pelizaeus-Merzb…

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Diseases / indications

• Pelizaeus-merzbacher Disease

Drugs mentioned

• ION356

Snippet

Sponsor: Ionis Pharmaceuticals, Inc. | Conditions: Pelizaeus-Merzbacher Disease | Phase 1 | Status: RECRUITING