Clinical Trial Update: UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells [Phase 1]

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Summary

Phase 1 trial evaluating intrathecal umbilical cord blood-derived oligodendrocyte-like cells for several inherited metabolic brain diseases; the study is curren…

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Diseases / indications

• Adrenoleukodystrophy
• Batten Disease
• Krabbe Disease
• Metachromatic Leukodystrophy
• Mucopolysaccharidosis Type Ii
• Niemann-pick Disease
• Pelizaeus-merzbacher Disease
• Sandhoff Disease

Drugs mentioned

• UCB-derived oligodendrocyte-like cells (intrathecal)

Snippet

Sponsor: Joanne Kurtzberg, MD | Conditions: Adrenoleukodystrophy, Batten Disease | Phase 1 | Status: RECRUITING