Hemophilia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-03-30Clinical Trial Update: A Study to Learn About How Changing Therapy From Emicizumab to Marstacimab Affects People With the Severe Hemophilia A. [Phase 1]
A Phase 1 study evaluating the effects of switching from emicizumab to marstacimab in people with severe hemophilia A.
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CLINICAL_TRIALS research · 2026-03-30Clinical Trial Update: A Study to Learn About the Study Medicine -Hympavzi in Congenital Hemophilia Patients Without Inhibitors in Japan.
A clinical trial to study Hympavzi in congenital hemophilia A or B patients without inhibitors in Japan; the study is currently active but n…
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CLINICAL_TRIALS research · 2026-03-24Clinical Trial Update: Long-term Study Evaluating Joint Health in People With Haemophilia A Receiving Real-world Prophylactic Treatment With Efanesoctocog Alfa [Phase 4]
This is a Phase 4 clinical trial update evaluating long-term joint health in people with Hemophilia A who are receiving real-world prophylax…
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CLINICAL_TRIALS trial_result · 2026-03-24Clinical Trial Update: Blood Flow Restriction in Improving Muscle Strength of Patients With Hemophilic Ankle Arthropathy [NA]
A completed clinical trial evaluated blood flow restriction as a method to improve muscle strength in patients with hemophilia-related ankle…
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CLINICAL_TRIALS research · 2026-03-23Clinical Trial Update: Monitoring of Anti-TFPI in Hemophilia
A clinical trial is monitoring an anti-TFPI therapy for hemophilia, and the study is currently recruiting.
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CLINICAL_TRIALS trial_result · 2026-03-20Clinical Trial Update: Open-Label Single Ascending Dose of Adeno-associated Virus Serotype 8 Factor IX Gene Therapy in Adults With Hemophilia B [Phase 1, Phase 2]
This open-label study investigates a single ascending dose of an adeno-associated virus serotype 8-based factor IX gene therapy in adults wi…
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EMA approval · 2026-03-19EMA Authorised: Hympavzi (marstacimab) — Pfizer Europe MA EEIG
The EMA authorised Hympavzi (marstacimab) for treatment of hemophilia A and hemophilia B.
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CLINICAL_TRIALS trial_result · 2026-03-19Clinical Trial Update: Phase 3 Study for Efficacy and Safety Outcomes Data in Japanese Patients With Severe Hemophilia A [Phase 3]
BioMarin's Phase 3 trial evaluating efficacy and safety outcomes of valoctocogene roxaparvovec in Japanese patients with severe Hemophilia A…
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CLINICAL_TRIALS trial_result · 2026-03-19Clinical Trial Update: A 48-Month Study to Evaluate Long-Term Effectiveness of Elocta on Joint Health
A 48-month trial is evaluating the long-term effectiveness of Elocta in maintaining joint health for individuals with Hemophilia A.
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CLINICAL_TRIALS research · 2026-03-19Clinical Trial Update: A Trial That Evaluates Disease Characteristics in Hemophilia B Adult Male Participants Receiving Prophylaxis With Standard of Care Factor IX Protein (FIX) Replacement Therapy
Clinical trial update describing a study that evaluates disease characteristics in adult male participants with Hemophilia B receiving proph…
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CLINICAL_TRIALS research · 2026-03-17Clinical Trial Update: Evaluation of the Safety and Efficacy of Hemophilia A Gene Therapy Drugs [Phase 2, Phase 3]
Ongoing Phase 2/Phase 3 clinical trials are evaluating the safety and efficacy of a gene therapy for Hemophilia A, sponsored by Shanghai Xin…
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CLINICAL_TRIALS research · 2026-03-17Clinical Trial Update: Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs) [Phase 3]
This Phase 3 trial evaluates the efficacy and safety of CSL222 (etranacogene dezaparvovec) gene therapy for adults with Hemophilia B who hav…
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CLINICAL_TRIALS research · 2026-03-11Clinical Trial Update: The CACHE Study: Coronary Artery Care in HaEmophilia
The CACHE Study is a recruiting clinical trial at Oxford University Hospitals NHS Trust evaluating coronary artery care in patients with Hem…
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CLINICAL_TRIALS trial_result · 2026-03-10Clinical Trial Update: A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency) [Phase 1]
Phase 1 clinical trial evaluating SR604 for safety, tolerability, pharmacokinetics, and pharmacodynamics in healthy participants and in pati…
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CLINICAL_TRIALS research · 2026-03-06Clinical Trial Update: EPOCH-Economics and Patient Outcomes in China in Haemophilia
This clinical trial update discusses the EPOCH economic analysis and patient outcomes in China for hemophilia, with the study currently acti…
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CLINICAL_TRIALS trial_result · 2026-03-05Clinical Trial Update: 3D Ultrasound in Hemophilic Ankles [NA]
A clinical trial from The Hospital for Sick Children evaluating 3D ultrasound in hemophilic ankles is not yet recruiting.
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EMA approval · 2026-03-04EMA Authorised: Hemgenix (Etranacogene dezaparvovec) — CSL Behring GmbH
The EMA authorised Hemgenix (etranacogene dezaparvovec) from CSL Behring for hemophilia B. The approval is conditional and carries orphan me…
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CLINICAL_TRIALS trial_result · 2026-03-04Clinical Trial Update: Dosage and PD Study of Eftrenonacog-alfa
Completed clinical trial update evaluating dosage and pharmacodynamics of Alprolix (eftrenonacog-alfa) for hemophilia B.
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CLINICAL_TRIALS trial_result · 2026-03-02Clinical Trial Update: Individualized Exercise Combined With Manual Therapy in Severe Hemophilia Patients With Polyarthropathy [NA]
The clinical trial evaluating individualized exercise combined with manual therapy for severe hemophilia with polyarthropathy has completed.
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CLINICAL_TRIALS research · 2026-02-27Clinical Trial Update: Efficacy and Safety Evaluation Study of SCT800 in Previously Untreated Hemophilia A Patients. [Phase 3]
A Phase 3 clinical trial evaluating the efficacy and safety of SCT800 in previously untreated patients with Hemophilia A is currently recrui…
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CLINICAL_TRIALS trial_result · 2026-02-27Clinical Trial Update: Low-Cost Platelet-Rich Plasma for Hemarthropathy [NA]
A completed clinical trial from the University of Utah evaluating low-cost platelet-rich plasma for hemarthrosis in hemophilia patients; res…
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CLINICAL_TRIALS trial_result · 2026-02-27Clinical Trial Update: Real-World Joint Outcomes After Selective Transition to Low-Dose Emicizumab in Pediatric Hemophilia A [Phase 2, Phase 3]
An update on a pediatric Hemophilia A trial examining real-world joint outcomes after a selective transition to low-dose emicizumab. The stu…
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FDA approval · 2026-02-27FDA Approved: DESMOPRESSIN ACETATE — Original Application (Caplin Steriles Limited)
FDA approved Desmopressin Acetate from Caplin Steriles Limited under an Original Application (ANDA). This marks the approval of a generic De…
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FDA approval · 2026-02-25FDA Approved: DESMODA — Original Application (Eton Pharmaceuticals, Inc.)
FDA approves DESMODA (desmopressin acetate oral solution) under an original NDA from Eton Pharmaceuticals; the product provides a new oral f…
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CLINICAL_TRIALS trial_result · 2026-02-20Clinical Trial Update: Central Sensitisation in Patients With Haemophilia and Degenerative Arthropathy
Update on a clinical trial investigating central sensitisation in patients with hemophilia; the study has completed.