Clinical Trial Update: Open-Label Single Ascending Dose of Adeno-associated Virus Serotype 8 Factor IX Gene Therapy in Adults With Hemophilia B [Phase 1, Phase 2]

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Summary

This open-label study investigates a single ascending dose of an adeno-associated virus serotype 8-based factor IX gene therapy in adults with Hemophilia B, con…

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Diseases / indications

• Hemophilia

Drugs mentioned

• AAV8 Factor IX gene therapy (AAV8-based factor IX gene therapy)

Snippet

Sponsor: Baxalta now part of Shire | Conditions: Hemophilia B | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING