Hemophilia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-02-20Clinical Trial Update: Validity and Reliability of the Two-minute Step Test in Hemophilia
A clinical trial evaluating the validity and reliability of the Two-minute Step Test in people with hemophilia; the study is currently not y…
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CLINICAL_TRIALS trial_result · 2026-02-20Clinical Trial Update: Incidence of Ultrasonographically Detected Articular Damage in Initially Healthy Joints of Patients With Hemophilia A Receiving Prophylactic Treatment With Emicizumab
A clinical trial update examining the incidence of ultrasound-detected articular damage in initially healthy joints of patients with Hemophi…
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CLINICAL_TRIALS research · 2026-02-20Clinical Trial Update: Effectiveness of an Educational Program for Pain Management in Patients With Hemophilic Arthropathy [NA]
This clinical trial aims to evaluate the effectiveness of an educational program for pain management in patients with hemophilia-related art…
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CLINICAL_TRIALS research · 2026-02-19Clinical Trial Update: An Observational Cohort Study to Characterize the Effectiveness and Safety of HEMGENIX® in Patients With Hemophilia B
An observational cohort study is being conducted to characterize the effectiveness and safety of Hemgenix in patients with Hemophilia B.
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CLINICAL_TRIALS trial_result · 2026-02-18Clinical Trial Update: A Long-term Study of ADYNOVI/ADYNOVATE in Participants With Haemophilia A
A long-term extension trial of ADYNOVI and ADYNOVATE in participants with Hemophilia A is currently active but not recruiting, sponsored by …
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CLINICAL_TRIALS research · 2026-02-18Clinical Trial Update: SAFE Study: Safety of aPCC Following Emicizumab Prophylaxis [Phase 3]
Phase 3 clinical trial assessing the safety of activated prothrombin complex concentrate after emicizumab prophylaxis in people with Hemophi…
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CLINICAL_TRIALS research · 2026-02-18Clinical Trial Update: Pharmacokinetic Comparison of Efanesoctocog Alfa vs Other EHL-rFVIII Products in Participants With Severe Haemophilia A [Phase 1]
Phase 1 pharmacokinetic comparison of efanesoctocog alfa versus other extended-half-life recombinant FVIII products in participants with sev…
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CLINICAL_TRIALS research · 2026-02-17Clinical Trial Update: Hemophilia A Research Program
A University of Washington-sponsored research program for Hemophilia A (severe) is currently recruiting participants to study new approaches…
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CLINICAL_TRIALS research · 2026-02-13Clinical Trial Update: Compassionate Use of Concizumab if You Have Haemophilia
This clinical trial update covers compassionate use of concizumab for individuals with congenital hemophilia.
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CLINICAL_TRIALS research · 2026-02-12Clinical Trial Update: PCC Treatment for Hemophilia Patients With Inhibitor（2022PCC-A） [Phase 4]
Phase 4 clinical trial evaluating Prothrombin Complex Concentrate (PCC) for hemophilia patients with inhibitors; currently recruiting.
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CLINICAL_TRIALS research · 2026-02-12Clinical Trial Update: National Longitudinal Cohort of Hematological Diseases
Recruiting for a national longitudinal cohort study of hematological diseases sponsored by the Institute of Hematology & Blood Diseases Hosp…
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CLINICAL_TRIALS research · 2026-02-04Clinical Trial Update: A Study to Test a Medicine (Fitusiran) Injected Under the Skin for Preventing Bleeding Episodes in Male Adolescent or Adult Participants With Severe Hemophilia [Phase 3]
This is a Phase 3 trial update for subcutaneous fitusiran to prevent bleeding episodes in males with severe hemophilia, with the study curre…
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CLINICAL_TRIALS trial_result · 2026-02-03Clinical Trial Update: Resistance Training With Blood Flow Restriction in Hemophilia [NA]
This ClinicalTrials.gov update reports the completion of a study evaluating resistance training with blood flow restriction in people with h…
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CLINICAL_TRIALS research · 2026-02-02Clinical Trial Update: COVID-19 Related Lockdown Effects On Chronic Diseases
This clinical trial update reports on the effects of COVID-19 lockdown on the management of several chronic diseases. The study encompasses …
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CLINICAL_TRIALS trial_result · 2026-01-26Clinical Trial Update: A Study to Evaluate Overall Health, Physical Activity, and Joint Outcomes in Participants With Severe or Moderate Hemophilia A Without Factor VIII Inhibitors on Emicizumab Prophylaxis [Phase 4]
A Phase 4 clinical trial update describing a study to evaluate overall health, physical activity, and joint outcomes in people with Hemophil…
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CLINICAL_TRIALS research · 2026-01-23Clinical Trial Update: Oral Health Status and Oral Health Related Quality of Life in a Group pf Egyptian Hemophilic Children [NA]
This clinical trial from Cairo University evaluates oral health status and oral health-related quality of life in Egyptian children with hem…
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CLINICAL_TRIALS trial_result · 2026-01-20Clinical Trial Update: Goal Attainment and Physical Activity in People With Hemophilia A
This clinical trial update reports the termination of a Sanofi-sponsored study examining goal attainment and physical activity in people wit…
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CLINICAL_TRIALS research · 2026-01-16Clinical Trial Update: Prevention of Bleeding in Patients With Moderate and Severe Hemophilia A Playing Sports: A Comparison Between Factor VIII and Emicizumab Prophylaxis
A clinical trial is evaluating bleeding prevention in moderate-to-severe Hemophilia A patients who play sports, comparing Factor VIII prophy…
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EMA approval · 2026-01-14EMA Authorised: Roctavian (valoctocogene roxaparvovec) — BioMarin International Limited
The European Medicines Agency authorised Roctavian (valoctocogene roxaparvovec) from BioMarin International Limited as a conditional, orphan…
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CLINICAL_TRIALS trial_result · 2026-01-14Clinical Trial Update: Physiotherapy to Improve Balance and Walking Capacity in Hemophilia [NA]
A completed clinical trial evaluating physiotherapy to improve balance and walking capacity in people with hemophilia.
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CLINICAL_TRIALS trial_result · 2026-01-13Clinical Trial Update: Nuwiq Dosing and Outcomes In the ManagEment of Women/Girls With Haemophilia A Needing FVIII Treatment for Surgery [Phase 4]
This Phase 4 clinical trial update evaluates dosing of Nuwiq (octocog alfa) and related outcomes for surgical management in women and girls …
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CLINICAL_TRIALS trial_result · 2026-01-12Clinical Trial Update: A Long-Term Follow-Up Study in Severe Hemophilia A Subjects Who Received BMN 270 in a Prior BioMarin Clinical Trial (270-401)
Long-term follow-up study in severe Hemophilia A patients who previously received BMN 270; enrollment is by invitation.
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CLINICAL_TRIALS research · 2026-01-12Clinical Trial Update: SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors [Phase 4]
Clinical trial update for SEVENFACT in Phase 4 evaluating bleeding events in patients with Hemophilia A or B with inhibitors; recruitment is…
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CLINICAL_TRIALS research · 2026-01-12Clinical Trial Update: ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
Clinical trial update for ATHN Transcends, a natural history study of non-neoplastic hematologic disorders, currently recruiting.
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CLINICAL_TRIALS other · 2026-01-08Clinical Trial Update: Recombinant Fusion Protein Linking Coagulation Factor IX With Albumin (rIX-FP) in Chinese Subjects With Hemophilia B Previously Treated With FIX Therapy [Phase 3]
Clinical trial update for a Phase 3 study of rIX-FP (recombinant factor IX albumin fusion protein) in Chinese subjects with Hemophilia B. Th…