Hemophilia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Lentiviral FIX Gene Therapy [Phase 1]
A Phase 1 clinical trial evaluating a lentiviral FIX gene therapy for Hemophilia B is currently recruiting.
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Lentiviral FVIII Gene Therapy [Phase 1]
Phase 1 clinical trial evaluating a lentiviral factor VIII gene therapy for hemophilia A is currently recruiting.
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: A Research Study Looking at How Different Doses of Study Medicine (Inno8) Work in the Body of People With Haemophilia A [Phase 1]
This update describes a Phase 1 clinical trial evaluating different doses of Inno8 in participants with Hemophilia A to study how the drug b…
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Canadian CHO-KLAT/H-FIT Study - Quality of Life of, and Burden of Caring for, Persons With Hemophilia
This Canadian trial (CHO-KLAT/H-FIT) assesses quality of life and caregiver burden in persons with hemophilia and has completed.
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CLINICAL_TRIALS research · 2026-04-23Clinical Trial Update: To Evaluate the Safety and Efficacy of GS1191-0445 Injection in the Treatment of Severe Hemophilia A [Phase 1, Phase 2]
A clinical trial update on GS1191-0445 Injection to evaluate its safety and efficacy in hemophilia A (Phase 1/Phase 2; status not recruiting…
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CLINICAL_TRIALS research · 2026-04-23Clinical Trial Update: Phase III Clinical Trial of STSP-0601 for Injection in Hemophilia Patients [Phase 3]
A Phase 3 trial evaluating STSP-0601 for injection in hemophilia patients is currently recruiting; sponsor is Jiangsu BioJeTay Biotechnology…
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CLINICAL_TRIALS research · 2026-04-23Clinical Trial Update: A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B [Phase 3]
Phase 3 trial evaluating the efficacy and safety of Fitusiran prophylaxis in male participants aged 1 to less than 12 years with Hemophilia …
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CLINICAL_TRIALS research · 2026-04-23Clinical Trial Update: Study of a Smart Sharps Disposal Device in Patients With Hemophilia [NA]
Clinical trial update on a Smart Sharps Disposal Device for patients with Hemophilia A and B; the study is currently NOT_YET_RECRUITING.
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CLINICAL_TRIALS research · 2026-04-22Clinical Trial Update: Safety of KN057 Prophylaxis in Patients With Haemophilia A or B [Phase 3]
Phase 3 clinical trial update on the safety of KN057 prophylaxis in adults with hemophilia A or B; the study is currently recruiting.
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CLINICAL_TRIALS research · 2026-04-21Clinical Trial Update: ATHNdataset Registry
The ATHNdataset Registry is currently recruiting participants; sponsored by the American Thrombosis and Hemostasis Network, the registry cov…
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CLINICAL_TRIALS research · 2026-04-21Clinical Trial Update: Long-term Safety and Efficacy Study and Dose-Escalation Substudy of PF 06838435 in Individuals With Hemophilia B [Phase 2]
Pfizer's PF-06838435 is in a Phase 2 long-term safety and efficacy study with a dose-escalation substudy in people with Hemophilia B; the tr…
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CLINICAL_TRIALS research · 2026-04-21Clinical Trial Update: A Survey on the Success of Inhibitor Elimination Using Individualized Concentrate Selection and Controlled ITI
This clinical trial is actively recruiting to evaluate inhibitor elimination in Hemophilia A using individualized concentrate selection and …
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CLINICAL_TRIALS research · 2026-04-20Clinical Trial Update: Searching Patterns In the Robustness of Immunological FVIII Tolerance
Clinical trial update describing a study on immunological tolerance to Factor VIII in Hemophilia A; the trial is not yet recruiting.
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CLINICAL_TRIALS research · 2026-04-17Clinical Trial Update: Study to Test the Safety and How Well Patients With Severe Hemophilia A Respond to Treatment With BAY 2599023 (DTX 201), a Drug Therapy That Delivers a Healthy Version of the Defective Factor VIII Gene Into the Nucleus of Liver Cells Using an Altered, Non-infectious Virus (AAV) as a "Shuttle" [Phase 1, Phase 2]
An early-phase clinical trial update evaluating BAY 2599023 (DTX 201), a gene therapy that delivers a functional factor VIII gene using an a…
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CLINICAL_TRIALS research · 2026-04-16Clinical Trial Update: Phase 3, Open-label, Single-dose Study of CSL222 in Adolescent Male Subjects (≥ 12 to < 18 Years of Age) With Severe or Moderately Severe Hemophilia B [Phase 3]
Phase 3 open-label, single-dose study evaluating CSL222 in adolescent males (ages 12 to under 18) with severe or moderately severe Hemophili…
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CLINICAL_TRIALS research · 2026-04-15Clinical Trial Update: An Observational Study to Learn More About How Well Damoctocog Alfa Pegol Works in Previously Treated Children With Hemophilia A
This Bayer-sponsored observational study aims to evaluate how well damoctocog alfa pegol works in previously treated children with Hemophili…
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CLINICAL_TRIALS research · 2026-04-15Clinical Trial Update: A Study to Learn More About the Safety of Damoctocog-alfa-pegol When Used in Routine Medical Care in Korean Participants With Hemophilia A
Bayer is conducting a safety study of damoctocog alfa pegol in Korean participants with Hemophilia A, evaluating safety in routine medical c…
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CLINICAL_TRIALS research · 2026-04-15Clinical Trial Update: A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating the safety and effectiveness of REGV131-LNP1265, a coagulation factor IX gene insertion therapy, in pe…
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CLINICAL_TRIALS research · 2026-04-13Clinical Trial Update: A Clinical Study to Evaluate the Effects of NXT007 Compared to Factor VIII Prophylaxis in Participants With Hemophilia A [Phase 3]
A Phase 3 clinical trial evaluating NXT007 versus Factor VIII prophylaxis in Hemophilia A is currently recruiting.
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CLINICAL_TRIALS research · 2026-04-13Clinical Trial Update: An Observational Study Called JOIHA to Learn More About How Well the Treatment With Jivi Works to Prevent Problems With Joints in Adults With Hemophilia A.
JOIHA is an observational study assessing the effectiveness of Jivi in preventing joint problems in adults with Hemophilia A; the study is a…
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CLINICAL_TRIALS research · 2026-04-13Clinical Trial Update: Joint Health, Balance and Quality of Life in Adults With Hemophilia A
This clinical trial update indicates a study assessing joint health, balance, and quality of life in adults with Hemophilia A is currently r…
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CLINICAL_TRIALS research · 2026-04-09Clinical Trial Update: Study to Learn More About the Safety of Drug Jivi Over a Long Period of Time in Previously Treated Patients With Hemophilia A (Bleeding Disorder Resulting From a Lack of FVIII) Who Are Receiving Jivi Regularly at Their Treating Doctors to Prevent Bleeding
A long-term safety study update for Jivi (emicizumab) in patients with Hemophilia A who are already receiving Jivi to prevent bleeds.
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CLINICAL_TRIALS research · 2026-04-09Clinical Trial Update: Evaluating Effectiveness and Long Term Safety of Damoctocog Alfa Pegol in Patients, Who Have Been Diagnosed With Hemophilia A
This clinical trial update describes evaluating the effectiveness and long-term safety of damoctocog alfa pegol in people with Hemophilia A,…
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CLINICAL_TRIALS research · 2026-04-08Clinical Trial Update: Post Approval Observational Study to Learn More About How Safe Octocog Alfa is and How Well it Works in Patients With Severe Hemophilia A in India
A post-approval observational study in India to evaluate the safety and effectiveness of Octocog alfa (Kovaltry) in patients with severe Hem…
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CLINICAL_TRIALS research · 2026-04-08Clinical Trial Update: Central Pain Mechanisms and Clinical and Psychological Factors Associated With Pain Interference in Daily Life in Adults With Hemophilia and Hemophilic Arthropathy
This clinical trial update outlines a study evaluating central pain mechanisms and psychological factors related to pain interference in dai…