Hemophilia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2026-08-14Clinical Trial Results: Study of the Efficacy and Safety PF-06741086 in Adult and Teenage Participants With Severe Hemophilia A or Moderately Severe to Severe Hemophilia B [Phase 3]
Phase 3 trial results for PF-06741086 in adults and adolescents with severe Hemophilia A or moderately to severely severe Hemophilia B; stud…
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CLINICAL_TRIALS trial_result · 2026-07-31Clinical Trial Results: Safety and Efficacy of FVIIa to Prevent Excessive Bleeding in Hemophilia Patients With Inhibitors Undergoing Major Surgery [Phase 3]
Phase 3 trial evaluating the safety and efficacy of FVIIa to prevent excessive bleeding in hemophilia patients with inhibitors undergoing ma…
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EMA approval · 2026-07-16EMA Authorised: Elocta (efmoroctocog alfa) — Swedish Orphan Biovitrum AB (publ)
Authorisation granted for Elocta (efmoroctocog alfa) by EMA for Hemophilia A, manufacturer Swedish Orphan Biovitrum AB (publ).
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EMA approval · 2026-07-16EMA Authorised: Hympavzi (marstacimab) — Pfizer Europe MA EEIG
EMA authorised Hympavzi (marstacimab) for hemophilia A and B, expanding treatment options for these conditions.
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EMA approval · 2026-07-09EMA Authorised: Adynovi (rurioctocog alfa pegol) — Baxalta Innovations GmbH
EMA authorised Adynovi (rurioctocog alfa pegol) for Hemophilia A, issued by Baxalta Innovations GmbH.
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EMA approval · 2026-07-08EMA Authorised: Altuvoct (Efanesoctocog alfa) — Swedish Orphan Biovitrum AB (publ)
EU authorization of Altuvoct (efanesoctocog alfa) for Hemophilia A.
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EMA approval · 2026-07-06EMA Authorised: Altuvoct (Efanesoctocog alfa) — Swedish Orphan Biovitrum AB (publ)
EMA has authorised Altuvoct (efanesoctocog alfa) for Hemophilia A, marking an orphan medicine approval by Swedish Orphan Biovitrum AB (publ)…
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CLINICAL_TRIALS trial_result · 2026-06-12Clinical Trial Update: A Clinical Study of Recombinant Human Coagulation Factor VIII for Injection in Patients With Severe Hemophilia A [Phase 3]
Phase 3 clinical trial update for recombinant human coagulation factor VIII in patients with severe Hemophilia A.
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CLINICAL_TRIALS trial_result · 2026-04-27Clinical Trial Update: A Study to Evaluate Overall Health, Physical Activity, and Joint Outcomes in Participants With Severe or Moderate Hemophilia A Without Factor VIII Inhibitors on Emicizumab Prophylaxis [Phase 4]
Phase 4 clinical trial evaluating overall health, physical activity, and joint outcomes in people with severe or moderate Hemophilia A on em…
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EMA approval · 2026-04-24EMA Authorised: Advate (octocog alfa) — Takeda Manufacturing Austria AG
The EMA authorised Advate (octocog alfa) by Takeda Manufacturing Austria AG for Hemophilia A, with a decision dated 21 May 2025.
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Lentiviral FIX Gene Therapy [Phase 1]
A Phase 1 clinical trial evaluating a lentiviral FIX gene therapy for Hemophilia B is currently recruiting.
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CLINICAL_TRIALS trial_result · 2026-04-24Clinical Trial Update: Post-marketing Surveillance (Use Result Surveillance) With Refixia®
Completion of a post-marketing surveillance study of Refixia (recombinant factor IX-Fc fusion protein) in hemophilia B, summarizing observed…
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Lentiviral FVIII Gene Therapy [Phase 1]
Phase 1 clinical trial evaluating a lentiviral factor VIII gene therapy for hemophilia A is currently recruiting.
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: A Research Study Looking at How Different Doses of Study Medicine (Inno8) Work in the Body of People With Haemophilia A [Phase 1]
This update describes a Phase 1 clinical trial evaluating different doses of Inno8 in participants with Hemophilia A to study how the drug b…
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Canadian CHO-KLAT/H-FIT Study - Quality of Life of, and Burden of Caring for, Persons With Hemophilia
This Canadian trial (CHO-KLAT/H-FIT) assesses quality of life and caregiver burden in persons with hemophilia and has completed.
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CLINICAL_TRIALS research · 2026-04-23Clinical Trial Update: To Evaluate the Safety and Efficacy of GS1191-0445 Injection in the Treatment of Severe Hemophilia A [Phase 1, Phase 2]
A clinical trial update on GS1191-0445 Injection to evaluate its safety and efficacy in hemophilia A (Phase 1/Phase 2; status not recruiting…
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CLINICAL_TRIALS research · 2026-04-23Clinical Trial Update: Phase III Clinical Trial of STSP-0601 for Injection in Hemophilia Patients [Phase 3]
A Phase 3 trial evaluating STSP-0601 for injection in hemophilia patients is currently recruiting; sponsor is Jiangsu BioJeTay Biotechnology…
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CLINICAL_TRIALS research · 2026-04-23Clinical Trial Update: A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B [Phase 3]
Phase 3 trial evaluating the efficacy and safety of Fitusiran prophylaxis in male participants aged 1 to less than 12 years with Hemophilia …
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CLINICAL_TRIALS trial_result · 2026-04-23Clinical Trial Update: Recombinant Single-chain Factor VIII (rVIII-SingleChain) in Chinese Participants With Hemophilia A Previously Treated With FVIII Products [Phase 3]
Phase 3 trial evaluating recombinant single-chain Factor VIII (rVIII-SingleChain) in Chinese participants with congenital Hemophilia A who w…
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CLINICAL_TRIALS research · 2026-04-23Clinical Trial Update: Study of a Smart Sharps Disposal Device in Patients With Hemophilia [NA]
Clinical trial update on a Smart Sharps Disposal Device for patients with Hemophilia A and B; the study is currently NOT_YET_RECRUITING.
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CLINICAL_TRIALS research · 2026-04-22Clinical Trial Update: Safety of KN057 Prophylaxis in Patients With Haemophilia A or B [Phase 3]
Phase 3 clinical trial update on the safety of KN057 prophylaxis in adults with hemophilia A or B; the study is currently recruiting.
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CLINICAL_TRIALS research · 2026-04-21Clinical Trial Update: ATHNdataset Registry
The ATHNdataset Registry is currently recruiting participants; sponsored by the American Thrombosis and Hemostasis Network, the registry cov…
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CLINICAL_TRIALS research · 2026-04-21Clinical Trial Update: Long-term Safety and Efficacy Study and Dose-Escalation Substudy of PF 06838435 in Individuals With Hemophilia B [Phase 2]
Pfizer's PF-06838435 is in a Phase 2 long-term safety and efficacy study with a dose-escalation substudy in people with Hemophilia B; the tr…
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CLINICAL_TRIALS research · 2026-04-21Clinical Trial Update: A Survey on the Success of Inhibitor Elimination Using Individualized Concentrate Selection and Controlled ITI
This clinical trial is actively recruiting to evaluate inhibitor elimination in Hemophilia A using individualized concentrate selection and …
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CLINICAL_TRIALS research · 2026-04-20Clinical Trial Update: Searching Patterns In the Robustness of Immunological FVIII Tolerance
Clinical trial update describing a study on immunological tolerance to Factor VIII in Hemophilia A; the trial is not yet recruiting.