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CLINICAL_TRIALS trial_result · 2026-03-19

Clinical Trial Update: Phase 3 Study for Efficacy and Safety Outcomes Data in Japanese Patients With Severe Hemophilia A [Phase 3]

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Summary

BioMarin's Phase 3 trial evaluating efficacy and safety outcomes of valoctocogene roxaparvovec in Japanese patients with severe Hemophilia A has an update on it…

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Diseases / indications

Drugs mentioned

  • valoctocogene roxaparvovec (Roctavian) (valoctocogene roxaparvovec)

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: Hemophilia A | Phase 3 | Status: ACTIVE_NOT_RECRUITING