Wiskott-aldrich Syndrome
📧 Sign up to get email alerts when something new happens for Wiskott-aldrich Syndrome.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2026-01-15Clinical Trial Update: Allogeneic Hematopoietic Stem Cell Transplant for Patients With Primary Immune Deficiencies [NA]
This clinical trial investigates allogeneic hematopoietic stem cell transplantation as a treatment for primary immune deficiencies, includin…
-
CLINICAL_TRIALS trial_result · 2025-12-15Clinical Trial Update: Sequential Cadaveric Lung and Bone Marrow Transplant for Immune Deficiency Diseases [Phase 1, Phase 2]
This clinical trial update describes an early-phase study evaluating sequential cadaveric lung transplantation followed by bone marrow trans…
-
CLINICAL_TRIALS trial_result · 2025-08-14Clinical Trial Update: Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for the Wiskott-Aldrich Syndrome [Phase 1, Phase 2]
Phase 1/2 pilot and feasibility study of hematopoietic stem cell gene transfer for Wiskott-Aldrich Syndrome has completed.
-
CLINICAL_TRIALS trial_result · 2025-04-04Clinical Trial Update: Gene Therapy for Wiskott-Aldrich Syndrome [Phase 1, Phase 2]
Phase 1/2 gene therapy trial for Wiskott-Aldrich Syndrome completed with results posted on 2025-04-04.
-
CLINICAL_TRIALS trial_result · 2023-09-15Clinical Trial Update: Conditioning Regimen for Allogeneic Hematopoietic Stem-Cell Transplantation [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating conditioning regimens for allogeneic hematopoietic stem-cell transplantation has completed recruitment…
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS trial_result · 2021-06-03Clinical Trial Update: Gene Therapy for Wiskott-Aldrich Syndrome (WAS) [Phase 1, Phase 2]
Phase 1/2 clinical trial update on a gene therapy approach for Wiskott-Aldrich Syndrome has completed.
-
CLINICAL_TRIALS trial_result · 2021-06-03Clinical Trial Update: Long Term Safety Follow up of Haematopoietic Stem Cell Gene Therapy for the Wiskott Aldrich Syndrome [Phase 1, Phase 2]
Long-term safety follow-up study of haematopoietic stem cell gene therapy for Wiskott-Aldrich Syndrome, currently active but not recruiting.
-
CLINICAL_TRIALS trial_result · 2020-05-06Clinical Trial Update: Efficacy and Safety of Romiplostim Versus Eltrombopag in the Treatment of Thrombocytopenia in Patients With Wiskott-Aldrich Syndrome [Phase 2]
Phase 2 trial comparing romiplostim to eltrombopag for thrombocytopenia in Wiskott-Aldrich Syndrome; efficacy and safety data not disclosed …
-
CLINICAL_TRIALS trial_result · 2019-03-18Clinical Trial Update: Thrombocytopenia and Bleeding in Wiskott-Aldrich Syndrome (WAS) Patients [Phase 2]
Phase 2 clinical trial update addressing thrombocytopenia and bleeding in patients with Wiskott-Aldrich Syndrome; study terminated with post…
-
CLINICAL_TRIALS trial_result · 2018-12-12Clinical Trial Update: A Trial of Plerixafor/G-CSF as Additional Agents for Conditioning Before TCR Alpha/Beta Depleted HSCT in WAS Patients [Phase 2]
Phase 2 trial evaluating plerixafor/G-CSF as conditioning agents before TCR alpha/beta depleted HSCT in patients with Wiskott-Aldrich Syndro…
-
CLINICAL_TRIALS trial_result · 2018-05-22Clinical Trial Update: Gene Therapy for WAS [Phase 1, Phase 2]
Genethon's Phase 1/2 gene therapy trial for Wiskott-Aldrich Syndrome has completed.
-
CLINICAL_TRIALS trial_result · 2017-08-16Clinical Trial Update: Interleukin-2 Treatment for Wiskott-Aldrich Syndrome [Phase 1]
A Phase 1 clinical trial evaluating interleukin-2 therapy for Wiskott-Aldrich syndrome and X-linked thrombocytopenia has completed.
-
CLINICAL_TRIALS trial_result · 2017-06-27Clinical Trial Update: Post-transplant Cyclophosphamide in Wiskott-Aldrich Syndrome
This entry reports an update on a clinical trial evaluating post-transplant cyclophosphamide for patients with Wiskott-Aldrich Syndrome.
-
CLINICAL_TRIALS trial_result · 2017-04-26Clinical Trial Update: Haploidentical Hematopoietic Stem Cell Transplantation Patients With Wiskott-Aldrich Syndrome [Phase 1]
Phase 1 clinical trial evaluating haploidentical hematopoietic stem cell transplantation in patients with Wiskott-Aldrich syndrome.
-
CLINICAL_TRIALS trial_result · 2016-06-23Clinical Trial Update: Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells [Phase 1, Phase 2]
A completed Phase 1/2 clinical trial evaluated unrelated hematopoietic stem cell transplantation for several genetic blood cell disorders, i…
-
CLINICAL_TRIALS trial_result · 2016-06-17Clinical Trial Update: Related Hematopoietic Stem Cell Transplantation (HSCT) for Genetic Diseases of Blood Cells [Phase 2]
Phase 2 study evaluating related hematopoietic stem cell transplantation for several genetic blood disorders; the trial was terminated and r…
-
CLINICAL_TRIALS trial_result · 2015-03-09Clinical Trial Update: Alefacept and Allogeneic Hematopoietic Stem Cell Transplantation [NA]
Clinical trial update indicating termination of an Alefacept plus allogeneic hematopoietic stem cell transplantation study, with results pos…
-
CLINICAL_TRIALS trial_result · 2014-12-23Clinical Trial Update: A Study to Find Out How Safe and Effective Gammaplex® is in Young People With Primary Immunodeficiency [Phase 4]
Phase 4 study evaluating the safety and effectiveness of Gammaplex in youths with primary immunodeficiency disorders, including Common Varia…
-
CLINICAL_TRIALS trial_result · 2014-07-14Clinical Trial Update: Study of Reduced Toxicity Myeloablative Conditioning Regimen for Wiskott-Aldrich Syndrome (WAS) [Phase 1, Phase 2]
A completed Phase 1/2 clinical trial evaluating a reduced-toxicity myeloablative conditioning regimen for Wiskott-Aldrich Syndrome.
-
CLINICAL_TRIALS trial_result · 2013-07-02Clinical Trial Update: Allogeneic SCT Of Pts With SCID And Other Primary Immunodeficiency Disorders [Phase 1, Phase 2]
This clinical trial update reports on allogeneic stem cell transplantation in patients with severe combined immunodeficiency and other prima…
-
CLINICAL_TRIALS trial_result · 2010-01-28Clinical Trial Update: Efficacy, Safety and Pharmacokinetics of Gammaplex in Primary Immunodeficiency Diseases. [Phase 3]
Phase 3 study evaluating the efficacy, safety, and pharmacokinetics of Gammaplex in primary immunodeficiency diseases completed with results…
-
CLINICAL_TRIALS trial_result · 2009-10-15Clinical Trial Update: Allogeneic Bone Marrow Transplantation in Patients With Primary Immunodeficiencies [NA]
This clinical trial update notes termination of an allogeneic bone marrow transplantation study for patients with primary immunodeficiencies…
-
CLINICAL_TRIALS trial_result · 2009-09-25Clinical Trial Update: Rapid Infusion of Immune Globulin Intravenous (Human) In Primary Immunodeficiency Patients [Phase 3]
A Phase 3 trial assessing rapid infusion of intravenous immunoglobulin (IVIG) in patients with primary immunodeficiency has completed.