CLINICAL_TRIALS
trial_result
· 2025-08-14
Clinical Trial Update: Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for the Wiskott-Aldrich Syndrome [Phase 1, Phase 2]
Summary
Phase 1/2 pilot and feasibility study of hematopoietic stem cell gene transfer for Wiskott-Aldrich Syndrome has completed.
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Snippet
Sponsor: David Williams | Conditions: Wiskott-Aldrich Syndrome | Phase 1, Phase 2 | Status: COMPLETED