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CLINICAL_TRIALS trial_result · 2025-08-14

Clinical Trial Update: Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for the Wiskott-Aldrich Syndrome [Phase 1, Phase 2]

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Summary

Phase 1/2 pilot and feasibility study of hematopoietic stem cell gene transfer for Wiskott-Aldrich Syndrome has completed.

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Diseases / indications

Drugs mentioned

  • Hematopoietic stem cell gene transfer

Snippet

Sponsor: David Williams | Conditions: Wiskott-Aldrich Syndrome | Phase 1, Phase 2 | Status: COMPLETED