CLINICAL_TRIALS trial_result · 2025-04-04

Clinical Trial Update: Gene Therapy for Wiskott-Aldrich Syndrome [Phase 1, Phase 2]

Phase 1/2 gene therapy trial for Wiskott-Aldrich Syndrome completed with results posted on 2025-04-04.

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Sponsor: Fondazione Telethon | Conditions: Wiskott-Aldrich Syndrome (WAS) | Phase 1, Phase 2 | Status: COMPLETED | Results posted: 2025-04-04