Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS trial_result · 2016-06-23

Clinical Trial Update: Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells [Phase 1, Phase 2]

View source ↗

Summary

A completed Phase 1/2 clinical trial evaluated unrelated hematopoietic stem cell transplantation for several genetic blood cell disorders, including sickle cell…

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Snippet

Sponsor: Children's Hospital Los Angeles | Conditions: Sickle Cell Disease, Thalassemia | Phase 1, Phase 2 | Status: COMPLETED