Records containing: Thalassemia
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CLINICAL_TRIALS study record update · 2026-04-08Pre-Transplant Immune Suppression With Hematopoietic Cell Transplantation From Haploidentical Donors for Adults and Children With Sickle Cell Disease or ß-Thalassemia (Haplo PTCy)
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CLINICAL_TRIALS study record update · 2026-03-25A Long-term Follow-up Study of Subjects With β-thalassemia or Sickle Cell Disease Treated With Autologous CRISPR-Cas9 Modified Hematopoietic Stem Cells (CTX001)
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CLINICAL_TRIALS study record update · 2026-03-24An Open-label, Multi-centre, Rollover Study to Characterise Long-term Safety and Efficacy of Etavopivat in Adults, Adolescents and Children Who Have Sickle Cell Disease or Thalassaemia and Have Completed a Treatment Period in an Etavopivat Study
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CLINICAL_TRIALS study record update · 2026-03-23A Phase 3b Study to Evaluate Efficacy and Safety of a Single Dose of Autologous CRISPR Cas9 Modified CD34+ Human Hematopoietic Stem and Progenitor Cells (CTX001) in Subjects With Transfusion-Dependent β-Thalassemia or Severe Sickle Cell Disease
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CLINICAL_TRIALS study record update · 2026-03-16Open Label, Multi-center, Phase IV Study of Ruxolitinib or Ruxolitinib and Panobinostat Combination, for Patients Who Have Completed Prior Global Novartis or Incyte Sponsored Studies
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CLINICAL_TRIALS study record update · 2026-03-06Combined Haploidentical Reduced Intensity Bone Marrow and Kidney Transplantation for Patients With Chronic Kidney Disease and Advanced Hematological Disorders
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CLINICAL_TRIALS study record update · 2026-03-05Pilot Study to Evaluate the Safety and Feasibility of Induction of Mixed Chimerism in Sickle Cell Disease Patients With COH-MC-17: a Non-Myeloablative, Conditioning Regimen and CD4+ T-cell-depleted Haploidentical Hematopoietic Transplant
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CLINICAL_TRIALS study record update · 2026-03-03A Phase 3 Study to Evaluate the Safety and Efficacy of a Single Dose of CTX001 in Pediatric Subjects With Transfusion-Dependent β-Thalassemia
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CLINICAL_TRIALS study record update · 2026-02-24Atrial Fibrillation in Beta-Thalassemia
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CLINICAL_TRIALS study record update · 2026-02-24Determination of Red Cell Survival in Sickle Cell Disease and Other Hemoglobinopathies Using Biotin Labeling
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CLINICAL_TRIALS study record update · 2026-02-05Multicenter Observational Study on Myocardial Iron Overload in 3 Multitransfused Populations
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CLINICAL_TRIALS study record update · 2026-01-20Evaluation of the Quality of Life in Patients With Chronic Iron Overload Due to Hemoglobinopathies in Greece, Who Are Under Treatment With Deferasirox, Based on Standard Clinical Practice.
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CLINICAL_TRIALS study record update · 2026-01-12ATHN Transcends: A Natural History Cohort Study of the Safety, Effectiveness, and Practice of Treatment in People With Non-Neoplastic Hematologic Disorders
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CLINICAL_TRIALS study record update · 2026-01-02A Study to Assess the Effect of Etavopivat on Cardiac Repolarisation in Healthy Participants
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CLINICAL_TRIALS study record update · 2025-12-29A Single-centre, Open-label, Single-group Study Investigating the Pharmacokinetics, Safety and Tolerability After a Single Dose of Oral Etavopivat in Healthy Chinese Participants
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CLINICAL_TRIALS study record update · 2025-12-17A Phase 1/2/3 Study of the Safety and Efficacy of a Single Dose of Autologous CRISPR-Cas9 Modified CD34+ Human Hematopoietic Stem and Progenitor Cells (hHSPCs) in Subjects With Transfusion-Dependent β-Thalassemia
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CLINICAL_TRIALS study record update · 2025-12-16A Phase 2 Open-Label Study to Evaluate Safety and Clinical Activity of Etavopivat in Patients With Thalassemia or Sickle Cell Disease
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CLINICAL_TRIALS study record update · 2025-10-07The Effect of Glutamine on Reducing Pulmonary Arterial Pressure in Non-transfusion-dependent Thalassemia Patients: a Single Blind Randomized Clinical Trial
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CLINICAL_TRIALS study record update · 2025-08-01Evaluating the Potential of Virtual Reality in Alleviating Pain and Anxiety Among Thalassemia Patients During Intravenous Cannulation: A Crossover Clinical Trial
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CLINICAL_TRIALS study record update · 2025-07-15Effect of Aerobic Exercise Paired With Strength Conditioning on Bone Health in Patients With Thalassemia
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CLINICAL_TRIALS study record update · 2025-03-21Pregnancy and Childbirth in Women with Thalassemia Yesterday and Today: a Multicentre Observational Study
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CLINICAL_TRIALS study record update · 2025-03-21Safety and Efficacy of Immunomodulator Drug Thalidomide in Multi-transfused Thalassemia Patients: A Single Center Experience From South Punjab, Pakistan
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CLINICAL_TRIALS study record update · 2025-03-14Phase IIb Clinical Study to Assess the Safety and Efficacy of CN128 Tablets in the Treatment of Iron Overload in Transfusion Dependent Thalassemia With Sever Liver Iron Overloaded Patients Aged 16 and Above
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CLINICAL_TRIALS study record update · 2025-03-05Testing a Natural Polyphenol Supplement to Inhibit Dietary Iron Absorption in Thai Adults with Iron-loading Thalassemia: a Stable Isotope Study
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CLINICAL_TRIALS study record update · 2025-01-30Development of THALEA (Thalassemia Education and Awareness) Kit and a Cluster Randomised Control Trial to Evaluate Its Effectiveness on Knowledge, Attitude, and Intention Regarding Premarital Thalassemia Screening Among Private Secondary School Students of Klang Valley, Malaysia