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A Phase 1/2/3 Study of the Safety and Efficacy of a Single Dose of Autologous CRISPR-Cas9 Modified CD34+ Human Hematopoietic Stem and Progenitor Cells (hHSPCs) in Subjects With Transfusion-Dependent β-Thalassemia

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Record identity and dates

Source
ClinicalTrials.gov
Source record ID
NCT03655678
Title field or adapter rule
protocolSection.identificationModule.officialTitle
Ingested At
2026-04-25T22:28:48.225409+00:00
Published At
2025-12-17T00:00:00+00:00
Record Updated At
2025-12-17
Timestamp Basis
source retrieval time was not retained by the feed adapter
Date limitation
source retrieval time was not retained by the feed adapter

Fields recorded by this source

protocolSection.conditionsModule.conditions
["Beta-Thalassemia", "Thalassemia", "Genetic Diseases, Inborn", "Hematologic Diseases", "Hemoglobinopathies"]
protocolSection.statusModule.lastUpdatePostDateStruct.date
"2025-12-17"
protocolSection.identificationModule.nctId
"NCT03655678"
protocolSection.identificationModule.officialTitle
"A Phase 1/2/3 Study of the Safety and Efficacy of a Single Dose of Autologous CRISPR-Cas9 Modified CD34+ Human Hematopoietic Stem and Progenitor Cells (hHSPCs) in Subjects With Transfusion-Dependent \u03b2-Thalassemia"
protocolSection.statusModule.overallStatus
"COMPLETED"
protocolSection.designModule.phases
["PHASE2", "PHASE3"]
protocolSection.statusModule.resultsFirstPostDateStruct.date
""

Study condition terms

  • Beta-Thalassemia (protocolSection.conditionsModule.conditions)
  • Thalassemia (protocolSection.conditionsModule.conditions)
  • Genetic Diseases, Inborn (protocolSection.conditionsModule.conditions)
  • Hematologic Diseases (protocolSection.conditionsModule.conditions)
  • Hemoglobinopathies (protocolSection.conditionsModule.conditions)

Intervention details are not present in the imported fields for this record. No drug-condition relationship is inferred from co-listing.

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