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CLINICAL_TRIALS ClinicalTrials.gov record update

A Phase 3b Study to Evaluate Efficacy and Safety of a Single Dose of Autologous CRISPR Cas9 Modified CD34+ Human Hematopoietic Stem and Progenitor Cells (CTX001) in Subjects With Transfusion-Dependent β-Thalassemia or Severe Sickle Cell Disease

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Record identity and dates

Source
ClinicalTrials.gov
Source record ID
NCT05477563
Title field or adapter rule
protocolSection.identificationModule.officialTitle
Ingested At
2026-04-25T22:28:09.332703+00:00
Published At
2026-03-23T00:00:00+00:00
Record Updated At
2026-03-23
Timestamp Basis
source retrieval time was not retained by the feed adapter
Date limitation
source retrieval time was not retained by the feed adapter

Fields recorded by this source

protocolSection.conditionsModule.conditions
["Beta-Thalassemia", "Thalassemia", "Hematologic Diseases", "Genetic Diseases, Inborn", "Hemoglobinopathies", "Sickle Cell Disease", "Sickle Cell Anemia"]
protocolSection.statusModule.lastUpdatePostDateStruct.date
"2026-03-23"
protocolSection.identificationModule.nctId
"NCT05477563"
protocolSection.identificationModule.officialTitle
"A Phase 3b Study to Evaluate Efficacy and Safety of a Single Dose of Autologous CRISPR Cas9 Modified CD34+ Human Hematopoietic Stem and Progenitor Cells (CTX001) in Subjects With Transfusion-Dependent \u03b2-Thalassemia or Severe Sickle Cell Disease"
protocolSection.statusModule.overallStatus
"RECRUITING"
protocolSection.designModule.phases
["PHASE3"]
protocolSection.statusModule.resultsFirstPostDateStruct.date
""

Study condition terms

  • Beta-Thalassemia (protocolSection.conditionsModule.conditions)
  • Thalassemia (protocolSection.conditionsModule.conditions)
  • Hematologic Diseases (protocolSection.conditionsModule.conditions)
  • Genetic Diseases, Inborn (protocolSection.conditionsModule.conditions)
  • Hemoglobinopathies (protocolSection.conditionsModule.conditions)
  • Sickle Cell Disease (protocolSection.conditionsModule.conditions)
  • Sickle Cell Anemia (protocolSection.conditionsModule.conditions)

Intervention details are not present in the imported fields for this record. No drug-condition relationship is inferred from co-listing.

This index keeps the source fields it imported; it may not contain the complete original record. Verify wording and context in the linked source.