Thalassemia
📧 Sign up to get email alerts when something new happens for Thalassemia.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS research · 2026-04-23Clinical Trial Update: Autologous Testicular Tissue Transplantation [NA]
Recruitment is ongoing for an autologous testicular tissue transplantation trial addressing cancer and hematologic diseases, including sickl…
-
CLINICAL_TRIALS research · 2026-03-24Clinical Trial Update: A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia [Phase 3]
This is an update on a Phase 3 clinical trial evaluating long-term treatment with etavopivat in people with Sickle Cell Disease or Thalassem…
-
CLINICAL_TRIALS trial_result · 2026-03-16Clinical Trial Update: CINC424A2X01B Rollover Protocol [Phase 4]
Phase 4 rollover protocol for CINC424A2X01B is active but not recruiting, spanning Primary Myelofibrosis, Polycythemia Vera, Graft-versus-ho…
-
CLINICAL_TRIALS research · 2026-03-03Clinical Trial Update: Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT) [Phase 3]
A Phase 3 clinical trial update reports ongoing evaluation of CTX001 for safety and efficacy in pediatric patients with transfusion-dependen…
-
CLINICAL_TRIALS research · 2026-02-24Clinical Trial Update: Determination of Red Cell Survival in Sickle Cell Disease and Other Hemoglobinopathies Using Biotin Labeling [EARLY_Phase 1]
This early-phase clinical trial aims to determine red blood cell survival in sickle cell disease and other hemoglobinopathies using biotin l…
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS research · 2026-02-24Clinical Trial Update: Atrial Fibrillation in Beta-Thalassemia
A recruiting clinical trial investigating atrial fibrillation in patients with beta-thalassemia.
-
CLINICAL_TRIALS trial_result · 2026-02-05Clinical Trial Update: Multicenter Observational Study on Myocardial Iron Overload in 3 Multitransfused Populations
A multicenter observational study assessing myocardial iron overload in three transfused populations has completed, focusing on patients wit…
-
CLINICAL_TRIALS research · 2026-01-20Clinical Trial Update: Evaluation of the Quality of Life in Patients With Chronic Iron Overload Due to Hemoglobinopathies in Greece.
Clinical trial evaluating quality of life in patients with chronic iron overload due to hemoglobinopathies in Greece, sponsored by Elpen Pha…
-
CLINICAL_TRIALS research · 2026-01-12Clinical Trial Update: ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
Clinical trial update for ATHN Transcends, a natural history study of non-neoplastic hematologic disorders, currently recruiting.
-
CLINICAL_TRIALS trial_result · 2026-01-02Clinical Trial Update: A Study on the Effect of Etavopivat on Heart Rhythm in Healthy Participants [Phase 1]
Phase 1 study of etavopivat assessing heart rhythm in healthy participants has completed; the trial also lists sickle cell disease and thala…
-
CLINICAL_TRIALS trial_result · 2025-12-29Clinical Trial Update: A Research Study Looking at a Single Dose of Etavopivat in Healthy Chinese Participants [Phase 1]
Phase 1 study evaluating a single dose of etavopivat in healthy Chinese participants has completed.
-
CLINICAL_TRIALS trial_result · 2025-12-17Clinical Trial Update: A Safety and Efficacy Study Evaluating CTX001 in Participants With Transfusion-Dependent β-Thalassemia [Phase 2, Phase 3]
A Phase 2/3 safety and efficacy study of CTX001 in transfusion-dependent beta-thalassemia has completed.
-
CLINICAL_TRIALS trial_result · 2025-12-16Clinical Trial Update: A Study of Etavopivat in Patients With Thalassemia or Sickle Cell Disease [Phase 2]
A Phase 2 study of etavopivat in patients with sickle cell disease and thalassemia has completed.
-
CLINICAL_TRIALS trial_result · 2025-10-10Clinical Trial Update: A Research Study of the Effect of Food on Etavopivat in Healthy Participants [Phase 1]
Phase 1 study assessing the effect of food on Etavopivat in healthy participants has been completed; the update focuses on pharmacokinetic i…
-
CLINICAL_TRIALS research · 2025-10-03Clinical Trial Update: Integrative Diagnosis for SCD and Other RADs
An ongoing clinical trial focused on integrative diagnosis for sickle cell disease and related red blood cell disorders, currently recruitin…
-
CLINICAL_TRIALS trial_result · 2025-09-25Clinical Trial Update: A Research Study of the Effect of Etavopivat on Other Drugs in Healthy Participants [Phase 1]
Completed Phase 1 study evaluating the effect of etavopivat on other drugs in healthy participants, sponsored by Novo Nordisk A/S.
-
CLINICAL_TRIALS research · 2025-07-15Clinical Trial Update: Effect of Exercise on Body Composition and Bone Health in Patients With Thalassemia [NA]
A UCSF-led clinical trial is recruiting to evaluate how exercise affects body composition and bone health in patients with thalassemia.
-
CLINICAL_TRIALS research · 2025-06-06Clinical Trial Update: Observational Study: Romiplostim for Platelet Recovery in Haploidentical HSCT
Observational study evaluating romiplostim to aid platelet recovery after haploidentical hematopoietic stem cell transplantation in children…
-
CLINICAL_TRIALS research · 2025-06-04Clinical Trial Update: Observational Study: Hetrombopag for Platelet Recovery in Haploidentical HSCT
An observational clinical trial registry entry evaluating hetrombopag for platelet recovery in children with thalassemia undergoing haploide…
-
CLINICAL_TRIALS trial_result · 2025-03-21Clinical Trial Update: Pregnancy and Childbirth in Women with Thalassemia Yesterday and Today
A completed clinical trial update examining pregnancy and childbirth in women with thalassemia, comparing past and present outcomes.
-
CLINICAL_TRIALS trial_result · 2025-03-21Clinical Trial Update: Safety and Efficacy of Immunomodulator Drug Thalidomide in Multi-transfused Thalassemia Patients [NA]
A completed clinical trial evaluating the safety and efficacy of thalidomide in multi-transfused thalassemia patients.
-
CLINICAL_TRIALS trial_result · 2025-03-14Clinical Trial Update: Long-term Clinical Study of CN128 in Thalassemia With Sever Liver Iron Overloaded Patients [Phase 2]
An update on the Phase 2 long-term study of CN128 in patients with thalassemia and severe liver iron overload, which has completed.
-
CLINICAL_TRIALS trial_result · 2025-03-05Clinical Trial Update: Inhibitory Effect of a Polyphenol Supplement on Dietary Iron Absorption in Adults with Thalassemia [NA]
A completed clinical trial evaluating whether a polyphenol supplement inhibits dietary iron absorption in adults with thalassemia and iron o…
-
CLINICAL_TRIALS research · 2025-01-30Clinical Trial Update: Development of THALEA Kit and Its Impact on Knowledge, Attitude, and Intention for Premarital Thalassemia Screening [NA]
This clinical trial update discusses the development of the THALEA kit and its potential impact on knowledge, attitudes, and intentions rega…
-
CLINICAL_TRIALS trial_result · 2024-12-19Clinical Trial Update: Haploidentical Hematopoietic Stem Cell Transplantation [Phase 1]
Phase 1 trial update reports the completion of a haploidentical hematopoietic stem cell transplantation study led by Catherine Bollard, inve…