Spinal Muscular Atrophy Type
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CLINICAL_TRIALS research · 2026-03-25Clinical Trial Update: A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy [Phase 2]
A Phase 2 clinical trial is evaluating how apitegromab works in subjects under 2 years old with spinal muscular atrophy (SMA). The study is …
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CLINICAL_TRIALS research · 2025-07-03Clinical Trial Update: Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 3 Patients [Phase 1, Phase 2]
An ongoing Phase 1/2 clinical trial is evaluating a gene therapy drug for Spinal Muscular Atrophy Type 3. The study is currently recruiting.
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CLINICAL_TRIALS research · 2025-07-03Clinical Trial Update: Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 2 Patients [Phase 1, Phase 2]
This entry reports on a Phase 1/2 clinical trial evaluating the safety and efficacy of a gene therapy drug in patients with spinal muscular …
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CLINICAL_TRIALS research · 2024-09-23Clinical Trial Update: Wearable Technology to Assess Gait Function in SMA and DMD
A completed clinical trial evaluating wearable technology to assess gait function in spinal muscular atrophy type 3 and Duchenne muscular dy…
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CLINICAL_TRIALS research · 2018-07-19Clinical Trial Update: Prospective Study of the Natural History of Patients With Type 2 and 3 Spinal Muscular Atrophy [NA]
This clinical trial update reports the completion of a prospective natural history study of patients with spinal muscular atrophy type 2 and…
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