CLINICAL_TRIALS
research
· 2025-07-03
Clinical Trial Update: Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 3 Patients [Phase 1, Phase 2]
Summary
An ongoing Phase 1/2 clinical trial is evaluating a gene therapy drug for Spinal Muscular Atrophy Type 3. The study is currently recruiting.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: GeneCradle Inc | Conditions: Spinal Muscular Atrophy Type 3 | Phase 1, Phase 2 | Status: RECRUITING