Spinal Muscular Atrophy Type
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-03-25Clinical Trial Update: A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy [Phase 2]
A Phase 2 clinical trial is evaluating how apitegromab works in subjects under 2 years old with spinal muscular atrophy (SMA). The study is …
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CLINICAL_TRIALS research · 2025-07-03Clinical Trial Update: Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 3 Patients [Phase 1, Phase 2]
An ongoing Phase 1/2 clinical trial is evaluating a gene therapy drug for Spinal Muscular Atrophy Type 3. The study is currently recruiting.
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CLINICAL_TRIALS research · 2025-07-03Clinical Trial Update: Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 2 Patients [Phase 1, Phase 2]
This entry reports on a Phase 1/2 clinical trial evaluating the safety and efficacy of a gene therapy drug in patients with spinal muscular …
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CLINICAL_TRIALS trial_result · 2025-05-25Clinical Trial Update: Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab [Phase 3]
Phase 3 extension study assessing long-term safety and efficacy of Apitegromab in spinal muscular atrophy patients who completed prior trial…
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CLINICAL_TRIALS research · 2024-09-23Clinical Trial Update: Wearable Technology to Assess Gait Function in SMA and DMD
A completed clinical trial evaluating wearable technology to assess gait function in spinal muscular atrophy type 3 and Duchenne muscular dy…
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CLINICAL_TRIALS trial_result · 2024-09-19Clinical Trial Update: The Effect of Spinal Orthosis on the Development of Scoliosis and Chest Deformity in Type I Spinal Muscular Atrophy [NA]
The clinical trial evaluating the use of spinal orthosis to affect the development of scoliosis and chest deformities in Spinal Muscular Atr…
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CLINICAL_TRIALS trial_result · 2024-07-22Clinical Trial Update: Body Weight Support Harness System in Spinal Muscular Atrophy [NA]
A clinical trial update notes that the body weight support harness system study in Spinal Muscular Atrophy Type I and Type II has completed.
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CLINICAL_TRIALS trial_result · 2023-11-30Clinical Trial Update: Long Term Safety of Amifampridine Phosphate in Spinal Muscular Atrophy 3 [Phase 2]
Phase 2 long-term safety trial of amifampridine phosphate in spinal muscular atrophy type 3 has been terminated with results posted.
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CLINICAL_TRIALS trial_result · 2023-10-11Clinical Trial Update: Safety and Efficacy Study of Pyridostigmine on Patients With Spinal Muscular Atrophy Type 3 [Phase 2]
A Phase 2 safety and efficacy study evaluating pyridostigmine in patients with Spinal Muscular Atrophy Type 3 has completed.
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CLINICAL_TRIALS trial_result · 2021-06-01Clinical Trial Update: Controlled Trial to Evaluate Amifampridine Phosphate in Spinal Muscular Atrophy Type 3 Patients [Phase 2]
Phase 2 trial evaluating amifampridine phosphate in spinal muscular atrophy type 3 patients has completed with posted results.
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CLINICAL_TRIALS trial_result · 2019-07-26Clinical Trial Update: Whole Body Vibration Therapy in Children With Spinal Muscular Atrophy [NA]
Clinical trial update for whole body vibration therapy in children with Spinal Muscular Atrophy Type 3; the study is terminated with results…
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CLINICAL_TRIALS research · 2018-07-19Clinical Trial Update: Prospective Study of the Natural History of Patients With Type 2 and 3 Spinal Muscular Atrophy [NA]
This clinical trial update reports the completion of a prospective natural history study of patients with spinal muscular atrophy type 2 and…