Clinical Trial Update: Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 2 Patients [Phase 1, Phase 2]

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Summary

This entry reports on a Phase 1/2 clinical trial evaluating the safety and efficacy of a gene therapy drug in patients with spinal muscular atrophy type 2. The …

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Diseases / indications

• Spinal Muscular Atrophy Type

Drugs mentioned

• Gene therapy drug

Snippet

Sponsor: GeneCradle Inc | Conditions: SMA II | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING