Records containing: Phenylketonuria
This is the wording recorded or indexed by the source. An agency index term is not necessarily an authorised indication. Co-listed drug names are not linked to this term as a treatment relationship.
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CLINICAL_TRIALS study record update · 2023-09-07Use of Dietary Protein and Free Fruits and Vegetables to Improve Metabolic Control Among Teens and Adults With Phenylketonuria: A Mixed Methods Approach
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CLINICAL_TRIALS study record update · 2023-08-16Hepatocyte Transplantation for Phenylketonuria
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CLINICAL_TRIALS study record update · 2023-08-14Evaluation of Behavior, Executive Function, Neurotransmitter Function and Genomic Expression in PKU "Nonresponders" to Kuvan® (Sapropterin Dihydrochloride)
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CLINICAL_TRIALS study record update · 2023-06-02An Exploratory Matched Case-control Study to Measure Blood Nutrient Levels of Adult PKU Patients on a Protein Substitute.
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CLINICAL_TRIALS study record update · 2023-04-24A Phase 4 Open-Label, Single-Cohort Study of the Long-Term Neurocognitive Outcomes in 4 to 5 Year-Old Children With Phenylketonuria Treated With Sapropterin Dihydrochloride (Kuvan®) for 7 Years
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CLINICAL_TRIALS study record update · 2023-03-07PICO: Phenylalanine and Its Impact on Cognition - Impact of Phenylalanine on Cognitive, Cerebral and Neurometabolic Parameters in Adult Patients With Phenylketonuria
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CLINICAL_TRIALS study record update · 2022-10-17An Open-label Study of the Efficacy and Safety of SYNB1618 and SYNB1934 in Patients With Phenylketonuria (SynPheny-1)
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CLINICAL_TRIALS study record update · 2022-10-12PKUDOS: Phenylketonuria (PKU) Demographic, Outcomes, and Safety Registry
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CLINICAL_TRIALS study record update · 2022-08-22Quantitative Requirements of Docosahexaenoic Acid for Neural Function in Children With Phenylketonuria
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CLINICAL_TRIALS study record update · 2022-06-30An Open-Label, Long-Term Follow Up Study of Safety and Efficacy in PKU Subjects With PAH Deficiency Previously Administered HMI 102
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CLINICAL_TRIALS study record update · 2022-04-27The Effectiveness of High-Dose Synthetic BH4 (Saproterin Dihydrochloride or "Kuvan") in Amish PKU Patients
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CLINICAL_TRIALS study record update · 2021-10-12Long-term Extension of a Phase 2, Open-Label Dose-Finding Study to Evaluate the Safety, Efficacy, and Tolerability of Multiple Subcutaneous Doses of rAvPAL-PEG in Subjects With PKU
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CLINICAL_TRIALS study record update · 2021-09-21Response to Phenylketonuria to Tetrahydrobiopterin (BH4)
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CLINICAL_TRIALS study record update · 2021-07-23A Phase 1, Randomized, Placebo- and Active-controlled Crossover Study to Evaluate the Effects of Sapropterin Dihydrochloride Oral Administration on QTc Intervals in Healthy Adult Subjects
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CLINICAL_TRIALS study record update · 2021-05-13A Phase 1/2a, First-in-human, Oral Single and Multiple Dose-escalation, Randomized, Double-blinded, Placebo-controlled Study of SYNB1618 in Healthy Adult Volunteers and Adult Subjects With Phenylketonuria to Evaluate Safety, Tolerability, Kinetics, and Pharmacodynamics
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CLINICAL_TRIALS study record update · 2020-12-22A Phase 3b Open-Label Study to Evaluate the Effect of Kuvan® on Neurocognitive Function, Maintenance of Blood Phenylalanine Concentrations, Safety, and Population Pharmacokinetics in Young Children With Phenylketonuria
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CLINICAL_TRIALS study record update · 2020-09-24Application of Stable Isotopes to Determine Protein Requirements in Children With Phenylketonuria (PKU)
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CLINICAL_TRIALS study record update · 2020-09-14A Phase 1, Multi-center, Randomized, Double-blind, Placebo-controlled, Cross-over Study to Evaluate the Pharmacodynamics, Safety, Tolerability and Pharmacokinetics of a Single Oral Dose of CDX-6114 in Patients With Phenylketonuria (PKU).
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CLINICAL_TRIALS study record update · 2020-06-04A Phase 3 Substudy to Evaluate Executive Function in Adults With Phenylketonuria Who Are Participating in the Phase 3 Study, 165-302
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CLINICAL_TRIALS study record update · 2019-10-08Kuvan Therapy in Phenylketonuria (PKU): The Effect of Blood Phenylalanine Concentration on Kuvan Response
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CLINICAL_TRIALS study record update · 2019-10-01Evaluating the Tolerance, Safety and Acceptability of PKU GMPro, a Whey Protein Derived Feed for the Dietary Management of Phenylketonuria in Children and Adults - a Pilot Trial
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CLINICAL_TRIALS study record update · 2019-02-27A Phase II, Multi-center, Open-label, Dose-finding Study to Evaluate Safety, Efficacy and Tolerability of Subcutaneously (SC) Administered rAvPAL-PEG in Patients With PKU for 24 Weeks
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CLINICAL_TRIALS study record update · 2019-02-26A Phase 2, Open-Label Study to Evaluate the Safety, Tolerability, and Efficacy of Subcutaneous Dose Levels of rAvPAL-PEG Administered Daily in Subjects With Phenylketonuria
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CLINICAL_TRIALS study record update · 2019-02-26Phase 2, Open-Label Dose-Finding Study to Evaluate the Safety, Efficacy, and Tolerability of Multiple Subcutaneous (SC) Doses of rAvPAL-PEG in Subjects With PKU
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CLINICAL_TRIALS study record update · 2018-10-19MRI Spectroscopy and Neuropsychological Functioning in Phenylketonuria