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CLINICAL_TRIALS trial_result · 2025-09-12

Clinical Trial Update: Study to Evaluate the Safety and Efficacy of Pegvaliase in Adolescents (Ages 12-17) With Phenylketonuria [Phase 3]

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Summary

Phase 3 trial evaluating pegvaliase for phenylketonuria in adolescents (ages 12-17) is currently active but not recruiting.

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Diseases / indications

Drugs mentioned

  • Pegvaliase (pegvaliase)

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: Phenylketonuria (PKU) | Phase 3 | Status: ACTIVE_NOT_RECRUITING