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CLINICAL_TRIALS research · 2025-12-01

Clinical Trial Update: Evaluation of BH4 Responsiveness in Our PKU Patients [Phase 1]

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Summary

Phase 1 clinical trial evaluating BH4 (tetrahydrobiopterin) responsiveness in phenylketonuria patients; the study is currently active but not recruiting.

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Diseases / indications

Drugs mentioned

  • tetrahydrobiopterin (tetrahydrobiopterin)

Snippet

Sponsor: Sohag University | Conditions: Phenylketonuria (PKU) | Phase 1 | Status: ACTIVE_NOT_RECRUITING