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CLINICAL_TRIALS trial_result · 2025-12-29

Clinical Trial Update: Preliminary Study of Brain Effects of Palynziq-Related Changes in Phenylalanine in Individuals With PKU

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Summary

This completed preliminary clinical trial evaluated how Palynziq-related changes in phenylalanine impact brain function in individuals with phenylketonuria.

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Diseases / indications

Drugs mentioned

  • PALYNZIQ (PEGVALIASE-PQPZ)

Snippet

Sponsor: University of Missouri-Columbia | Conditions: Phenylketonurias | Status: COMPLETED