Clinical Trial Update: AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom) [Phase 1, Phase 2]

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Summary

An adeno-associated virus (AAV) gene therapy study for adults with classic phenylketonuria (PKU) is in Phase 1/2 and currently recruiting.

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Diseases / indications

• Phenylketonuria

Drugs mentioned

• AAV gene therapy for Phenylketonuria (PHEdom) (AAV-mediated gene therapy)

Snippet

Sponsor: NGGT INC. | Conditions: Phenylketonurias | Phase 1, Phase 2 | Status: RECRUITING