Niemann-pick Disease
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-04-22Clinical Trial Update: Retinal Hyperspectral Imaging in Neurodegenerative Diseases [NA]
A clinical trial is investigating retinal hyperspectral imaging for neurodegenerative diseases and dementia, currently recruiting participan…
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CLINICAL_TRIALS research · 2025-09-08Clinical Trial Update: UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells [Phase 1]
Phase 1 trial evaluating intrathecal umbilical cord blood-derived oligodendrocyte-like cells for several inherited metabolic brain diseases;…
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CLINICAL_TRIALS research · 2025-05-22Clinical Trial Update: National Multicentre Study of the Natural History of Acid Sphingo-myelinase Deficiency in Adults and Children
A national multicentre observational study investigating the natural history of acid sphingomyelinase deficiency (ASMD) in adults and childr…
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CLINICAL_TRIALS research · 2017-04-04Clinical Trial Update: Investigating Lysosomal Storage Diseases in Minority Groups
A clinical trial update from O & O Alpan LLC examining lysosomal storage disorders in minority populations, including Gaucher disease, Fabry…
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CLINICAL_TRIALS research · 2008-03-04Clinical Trial Update: PET Scan of Brain Metabolism in Relation to Age and Disease
Completed clinical trial update describing PET imaging of brain metabolism across age and disease, including Alzheimer's disease, brain neop…
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