Clinical Trial Update: National Multicentre Study of the Natural History of Acid Sphingo-myelinase Deficiency in Adults and Children

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Summary

A national multicentre observational study investigating the natural history of acid sphingomyelinase deficiency (ASMD) in adults and children; the study is not…

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Diseases / indications

• Acid Sphingomyelinase Deficiency
• Niemann-pick Disease

Snippet

Sponsor: Wladimir MAUHIN, Dr | Conditions: Acid Sphingomyelinase Deficiency (ASMD), Niemann Pick Disease | Status: NOT_YET_RECRUITING