Niemann-pick Disease
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Sign up freeTop drugs studied for this disease
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EMA approval · 2026-07-09EMA Authorised: Zavesca (miglustat) — Advanz Pharma Limited
Authorization granted for Zavesca (miglustat) to Advanz Pharma Limited for Gaucher disease and Niemann-Pick diseases in the EU.
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EMA approval · 2026-01-28EMA Authorised: Zavesca (miglustat) — Janssen Cilag International NV
EMA authorised Zavesca (miglustat) for Gaucher disease and Niemann-Pick diseases; Janssen Cilag International NV is the marketing authorisat…