Records containing: Myotonic Dystrophy
This is the wording recorded or indexed by the source. An agency index term is not necessarily an authorised indication. Co-listed drug names are not linked to this term as a treatment relationship.
Follow recorded terms in Drug Alerts for Android. Free includes unlimited local condition follows and an on-open recent-record watchlist. Plus adds no ads and personal organization tools.
All
FDA submission records
EMA medicine records
ClinicalTrials.gov record updates
ClinicalTrials.gov records with results posted
-
CLINICAL_TRIALS study record update · 2026-09-01A Phase 3 Randomized, Double-Blind, Placebo-Controlled, Global Study to Evaluate the Efficacy and Safety of Intravenous AOC 1001 for the Treatment of Myotonic Dystrophy Type 1
-
CLINICAL_TRIALS study record update · 2026-04-23A Global Phase 3 Open-Label Extension Study to Assess the Long-Term Safety, Tolerability, and Efficacy of Intravenous AOC 1001 for the Treatment of Myotonic Dystrophy Type 1
-
CLINICAL_TRIALS study record update · 2026-04-23Evaluation of the Diagnostic Performance of Non-Invasive Prenatal Diagnosis for Single Gene Disorders
-
CLINICAL_TRIALS study record update · 2026-04-21A Phase 3, Randomized, Double-Blind, 48-Week Placebo-Controlled Study to Assess the Efficacy, Safety, and Tolerability of DYNE-101 Administered to Participants With Myotonic Dystrophy Type 1
-
CLINICAL_TRIALS study record update · 2026-03-19Evaluation of Arrhythmic Risk in Myotonic Dystrophy Type I (DM 1)
- Organize your saved records without ads with Plus.
-
CLINICAL_TRIALS study record update · 2026-03-12A Randomized, Double-Blind, Placebo-Controlled, Phase 1/2 Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Single and Multiple-Doses of AOC 1001 Administered Intravenously to Adult Myotonic Dystrophy Type 1 (DM1) Patients
-
CLINICAL_TRIALS study record update · 2026-02-06A Randomized, Double-Blind, Placebo-Controlled, Multi-Center Study to Investigate the Efficacy and Safety of Once Daily Mexiletine PR During 26 Weeks of Treatment in Patients With Myotonic Dystrophy Type 1 and Type 2 (Phase 3)
-
CLINICAL_TRIALS study record update · 2026-02-02A Phase 1/Phase 2 Open-label Single Arm Study With Dose Escalation (Part A), and Dose Expansion (Part B) Parts to Evaluate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants 10 to 50 Years Old With Non-congenital Myotonic Dystrophy Type 1
-
CLINICAL_TRIALS study record update · 2026-01-26An Open-Label Extension Study to Evaluate the Long-Term Safety and Efficacy of Once Daily Mexiletine PR in Patients With Myotonic Dystrophy Type 1 and Type 2 Who Have Completed the MEX-DM-302 Study (ATLAS Study)
-
CLINICAL_TRIALS study record update · 2026-01-23Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy (DeQoDE-DM)
-
CLINICAL_TRIALS study record update · 2026-01-22A Phase 3 Randomized, Double-Blind, Placebo-Controlled, Global Study to Evaluate the Efficacy and Safety of Intravenous AOC 1001 for the Treatment of Myotonic Dystrophy Type 1
-
CLINICAL_TRIALS study record update · 2026-01-07Assessment of a Portable Digital Device for Quantified Analysis of Markerless Walking in Volunteers With Neuromuscular Diseases or Asymptomatic Volunteers
-
CLINICAL_TRIALS study record update · 2025-11-24Extracellular RNA Biomarkers of Myotonic Dystrophy
-
CLINICAL_TRIALS study record update · 2025-11-24Biomarker Development for Muscular Dystrophies
-
CLINICAL_TRIALS study record update · 2025-10-15National Registry of Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Patients and Family Members
-
CLINICAL_TRIALS study record update · 2025-10-08A Phase 2 Extension Study to Evaluate the Long-Term Safety, Tolerability, Efficacy, Pharmacokinetics, and Pharmacodynamics of AOC 1001 Administered Intravenously to Adult Myotonic Dystrophy Type 1 (DM1) Patients
-
CLINICAL_TRIALS study record update · 2025-09-10Development and Validation of the FBIndex to Determine the Risk of Falls for Patients With Neuromuscular Disorders
-
CLINICAL_TRIALS study record update · 2025-07-30Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension
-
CLINICAL_TRIALS study record update · 2025-07-25An Observational Study to Describe the Long-term Safety and Effectiveness of Namuscla in the Symptomatic Management of Myotonia in Adult Patients With Non-dystrophic Myotonic Disorders
-
CLINICAL_TRIALS study record update · 2024-11-25An Open-label, Non-Comparative Study to Evaluate the Steady-State Pharmacokinetics, Safety, and Efficacy of Mexiletine in Adolescents and Children With Myotonic Disorders
-
CLINICAL_TRIALS study record update · 2024-11-21Myotonic Dystrophy Family Registry
-
CLINICAL_TRIALS study record update · 2024-09-19The FBIndex to Determine the Risk of Falls and Its Translation to Assistive Gait Device Care for Patients With Neuromuscular Disorders
-
CLINICAL_TRIALS study record update · 2024-04-18A Multi-Site Tissue Repository Providing Annotated Biospecimens for Approved Investigator-Directed Biomedical Research Initiatives
-
CLINICAL_TRIALS study record update · 2023-12-04The UK National Registry for Myotonic Dystrophy
-
CLINICAL_TRIALS study record update · 2021-06-23Double-Blind, Placebo-Controlled, Dose-Range-Finding, Crossover Trial of Single Day Administration of ERX-963 in Adults With Myotonic Dystrophy Type 1