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CLINICAL_TRIALS research · 2026-04-21

Clinical Trial Update: Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1 [Phase 3]

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Summary

Phase 3 clinical trial update indicates Dyne Therapeutics is evaluating Zeleciment Basivarsen (DYNE-101) for efficacy, safety, and tolerability in participants …

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Diseases / indications

Drugs mentioned

  • Zeleciment Basivarsen (basivarsen)

Snippet

Sponsor: Dyne Therapeutics | Conditions: Myotonic Dystrophy Type 1 (DM1), DM1 | Phase 3 | Status: RECRUITING