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CLINICAL_TRIALS research · 2025-07-30

Clinical Trial Update: Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

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Summary

This clinical trial extension outlines plans to assess endpoints and trial readiness for a pediatric myotonic dystrophy study. It targets congenital and childho…

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Diseases / indications

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Sponsor: Virginia Commonwealth University | Conditions: Congenital Myotonic Dystrophy, Childhood Myotonic Dystrophy | Status: RECRUITING