Monocarboxylate Transporter Deficiency
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CLINICAL_TRIALS research · 2026-04-20Clinical Trial Update: Expanded Access Program for Tiratricol in Patients With Monocarboxylate Transporter 8 Deficiency
Expanded access program update for tiratricol in patients with Monocarboxylate Transporter 8 deficiency (Allan-Herndon-Dudley Syndrome).
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CLINICAL_TRIALS withdrawal · 2026-04-08Clinical Trial Update: Withdrawal of Tiratricol Treatment in Males With Monocarboxylate Transporter 8 Deficiency (MCT8 Deficiency) [Phase 3]
A Phase 3 trial evaluating tiratricol for Monocarboxylate Transporter 8 Deficiency has involved withdrawal of tiratricol treatment in male p…
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CLINICAL_TRIALS trial_result · 2024-04-25Clinical Trial Update: MCT8 Deficiency Caregiver Study
This clinical trial update indicates that the caregiver study for Monocarboxylate Transporter 8 (MCT8) deficiency/Allan-Herndon-Dudley Syndr…
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CLINICAL_TRIALS trial_result · 2021-08-24Clinical Trial Update: Glycerol-Phenylbutyrate Treatment in Children With MCT Mutation (Allan-Herndon- Dudley Syndrome) [Phase 2, Phase 3]
Clinical trial update for glycerol-phenylbutyrate treatment in children with Monocarboxylate Transporter 8 deficiency (Allan-Herndon-Dudley …