Clinical Trial Update: Glycerol-Phenylbutyrate Treatment in Children With MCT Mutation (Allan-Herndon- Dudley Syndrome) [Phase 2, Phase 3]

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Summary

Clinical trial update for glycerol-phenylbutyrate treatment in children with Monocarboxylate Transporter 8 deficiency (Allan-Herndon-Dudley Syndrome) spanning P…

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Diseases / indications

• Monocarboxylate Transporter Deficiency

Drugs mentioned

• Glycerol phenylbutyrate (glycerol phenylbutyrate)

Snippet

Sponsor: Kaplan Medical Center | Conditions: Monocarboxylate Transporter 8 Deficiency | Phase 2, Phase 3 | Status: UNKNOWN