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CLINICAL_TRIALS withdrawal · 2026-04-08

Clinical Trial Update: Withdrawal of Tiratricol Treatment in Males With Monocarboxylate Transporter 8 Deficiency (MCT8 Deficiency) [Phase 3]

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Summary

A Phase 3 trial evaluating tiratricol for Monocarboxylate Transporter 8 Deficiency has involved withdrawal of tiratricol treatment in male participants.

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Diseases / indications

Drugs mentioned

  • tiratricol (tiratricol)

Snippet

Sponsor: Rare Thyroid Therapeutics International AB | Conditions: Monocarboxylate Transporter 8 Deficiency, Allan-Herndon-Dudley Syndrome | Phase 3 | Status: COMPLETED